Antisense Oligonucleotide Mediated Increase in OPA1 Improves Mitochondrial Function in Fibroblasts Derived from Patients with Autosomal Dominant Optic Atrophy (ADOA)

被引：0
|
作者：
Venkatesh, Aditya [1 ]
Ali, Syed [1 ]
Oh, Raymond S. [1 ]
Sonntag, Donna [1 ]
Li, Zhiyu [2 ]
McKenty, Taylor [1 ]
Slipp, Brittany A. [1 ]
Hufnagel, Robert B. [2 ]
Hoger, Jeffrey H. [1 ]
Liau, Gene [1 ]
机构：
[1] Stoke Therapeut, Bedford, MA USA
[2] NIH, Bldg 10, Bethesda, MD 20892 USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
443
引用
收藏
页码：215 / 215
页数：1
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