Antisense Oligonucleotide Mediated Increase in OPA1 Improves Mitochondrial Function in Fibroblasts Derived from Patients with Autosomal Dominant Optic Atrophy (ADOA)

被引：0

作者：

Venkatesh, Aditya ^{[1
]}

Ali, Syed ^{[1
]}

Oh, Raymond S. ^{[1
]}

Sonntag, Donna ^{[1
]}

Li, Zhiyu ^{[2
]}

McKenty, Taylor ^{[1
]}

Slipp, Brittany A. ^{[1
]}

Hufnagel, Robert B. ^{[2
]}

Hoger, Jeffrey H. ^{[1
]}

Liau, Gene ^{[1
]}

机构：

[1] Stoke Therapeut, Bedford, MA USA

[2] NIH, Bldg 10, Bethesda, MD 20892 USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

443

引用

页码：215 / 215

页数：1

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