RNA Targeting Gene Therapy Exon-Skipping Approach for the Treatment of Duchenne Muscular Dystrophy

被引：0
|
作者：
Lardelli, Rea [1 ]
Roth, Daniela Martino [1 ]
Geddes, Claire [1 ]
Nachtrab, Greg [1 ]
Wilson, Alistair [1 ]
Lee, Shawn [1 ]
Ross, Olivia [1 ]
Negraes, Priscilla Davidson [1 ]
Gibbs, Dan [1 ]
Zisoulis, Dimitrios [1 ]
Batra, Ranjan [1 ]
机构：
[1] LocanaBio, San Diego, CA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
413
引用
收藏
页码：201 / 201
页数：1
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