RNA Targeting Gene Therapy Exon-Skipping Approach for the Treatment of Duchenne Muscular Dystrophy

被引：0

作者：

Lardelli, Rea ^{[1
]}

Roth, Daniela Martino ^{[1
]}

Geddes, Claire ^{[1
]}

Nachtrab, Greg ^{[1
]}

Wilson, Alistair ^{[1
]}

Lee, Shawn ^{[1
]}

Ross, Olivia ^{[1
]}

Negraes, Priscilla Davidson ^{[1
]}

Gibbs, Dan ^{[1
]}

Zisoulis, Dimitrios ^{[1
]}

Batra, Ranjan ^{[1
]}

机构：

[1] LocanaBio, San Diego, CA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

413

引用

页码：201 / 201

页数：1

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