Small Nuclear RNA-Mediated Exon 51 Skipping AAV9 Gene Therapy for the Treatment of Duchenne Muscular Dystrophy

被引：0

作者：

Markmiller, Rea Lardelli ^{[1
]}

Nachtrab, Greg ^{[1
]}

Geddes, Claire ^{[1
]}

Tadokoro, Taka ^{[1
]}

Pasha, Sheik ^{[1
]}

Knowland, Daniel ^{[1
]}

Roth, Daniela ^{[1
]}

Carreno, Alberto ^{[1
]}

Villegas, Gustavo ^{[1
]}

Sarkar, Anindita ^{[1
]}

Reid, Derek ^{[1
]}

Nguyen, Lynn ^{[1
]}

Adams, Rachel ^{[1
]}

Diago, Oscar ^{[1
]}

Vakharia, Shruti ^{[1
]}

Almaguer, Bryan ^{[1
]}

Gutierrez, Haydee ^{[1
]}

Go, Yesol ^{[1
]}

Torres, Ronald ^{[1
]}

Narayan, Nandini ^{[1
]}

Vashist, Deepti ^{[1
]}

Berlin, Aaron ^{[1
]}

Tran, Amanda ^{[1
]}

Batra, Ranjan ^{[1
]}

Leonard, John E. ^{[1
]}

机构：

[1] Locanabio, San Diego, CA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1198

引用

页码：571 / 571

页数：1

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