A Phase IIb Placebo-Controlled Study of the Exon-Skipping Drug Eteplirsen in Subjects with Duchenne Muscular Dystrophy

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Mendell, Jerry
Rodino-Klapac, Louise
Sahenk, Zarife
Roush, Kandice
Bird, Lauren
Lowes, Linda
Alfano, Lindsay
Gomez, Ana Maria
Lewis, Sarah
Shontz, Kim
Flanigan, Kevin
Taylor, Laura
Walker, Christopher
Campbell, Katie
Allen, Hugh
Schilling, Christopher
Kean, John
Sazani, Peter
Kaye, Edward
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R74 [神经病学与精神病学];
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页码:E87 / E88
页数:2
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