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- [11] A phase II, open-label, extension study of long-term patisiran treatment in patients with hereditary transthyretin-mediated (hATTR) amyloidosisORPHANET JOURNAL OF RARE DISEASES, 2020, 15 (01)Coelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, Portugal Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalAdams, David论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, INSERM U1195, AP HP, Natl Reference Ctr Familial Amyloidot Polyneuropa, 78 Rue Gen Leclerc, F-94270 Le Kremlin Bicetre, France Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Hosp Santa Maria CHULN, Lisbon, Portugal Univ Lisbon, Fac Med, IMM, Lisbon, Portugal Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalWaddington-Cruz, Marcia论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Hosp Univ Clementino Fraga Filho, BR-21941913 Rio De Janeiro, RJ, Brazil Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalSchmidt, Hartmut H.论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Waldeyerstr 1, D-48149 Munster, Germany Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalBuades, Juan论文数: 0 引用数: 0 h-index: 0机构: Fundacio Inst Invest Sanitaria Illes Balears IdIS, Carretera Valldemossa 79, Palma De Mallorca 07120, Balearic Island, Spain Hosp Univ Son Llatzer, Serv Med Interna, Carretera Manacor KM 7198, Palma De Mallorca, Balearic Island, Spain Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalCampistol, Josep论文数: 0 引用数: 0 h-index: 0机构: Univ Barcelona, Hosp Clin, C Villarroel 170, Barcelona 8036, Spain Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, 72 East Concord St,K-504, Boston, MA 02118 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, 855 North Wolfe St,Rangos 435, Baltimore, MD 21205 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalWang, Jing Jing论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, 300 Third St, Cambridge, MA 02142 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, 300 Third St, Cambridge, MA 02142 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, 300 Third St, Cambridge, MA 02142 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalGollob, Jared论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, 300 Third St, Cambridge, MA 02142 USA Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, PortugalSuhr, Ole B.论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Univ Storget 16, S-90187 Umea, Sweden Ctr Hosp Porto, Hosp Santo Antonio, P-4099001 Porto, Portugal
- [12] HELIOS-A: RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHYJOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2022, 79 (09) : 302 - 302Gonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoAdams, David论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoTournev, Ivailo论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoTaylor, Mark论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoPlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoBerk, John论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoGillmore, Julian David论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoChen, Chongshu论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoBadri, Prajakta论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoVest, John论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico
- [13] Diagnostic delay in patients with sporadic hereditary transthyretin-mediated amyloidosisNEUROLOGICAL SCIENCES, 2025, 46 (02) : 929 - 934Antunes, Bernardo论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugal Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, PortugalConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugal ULS Santa Maria, Ctr Acad Med Lisboa, Dept Neurociencias & Saude Mental, Lisbon, Portugal Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugalde Campos, Catarina Falcao论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugal ULS Santa Maria, Ctr Acad Med Lisboa, Dept Neurociencias & Saude Mental, Lisbon, Portugal Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugalde Carvalho, Mamede论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugal ULS Santa Maria, Ctr Acad Med Lisboa, Dept Neurociencias & Saude Mental, Lisbon, Portugal Univ Lisbon, Fac Med, Ctr Estudos Egas Moniz, Inst Fisiol, Lisbon, Portugal
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- [17] Primary Results From Apollo-B, A Phase 3 Study Of Patisiran In Patients With Transthyretin-Mediated Amyloidosis With CardiomyopathyJOURNAL OF CARDIAC FAILURE, 2023, 29 (04) : 550 - 550Maurer, Mathew S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Med Ctr, New York, NY USA Columbia Univ, Med Ctr, New York, NY USAFontana, Marianna论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, London, England Columbia Univ, Med Ctr, New York, NY USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Simoes, Marcus论文数: 0 引用数: 0 h-index: 0机构: Univ Sao Paulo, Hosp Clin, Fac Med Ribeirao Preto, Ribeirao Preto, Brazil Columbia Univ, Med Ctr, New York, NY USAGrogan, Martha论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Coll Med, Rochester, MN USA Columbia Univ, Med Ctr, New York, NY USAFernandes, Fabio论文数: 0 引用数: 0 h-index: 0机构: HCFMUSP, Inst Coracao, Sao Paulo, Brazil Columbia Univ, Med Ctr, New York, NY USAGottlieb, Robert L.论文数: 0 引用数: 0 h-index: 0机构: Baylor Univ, Med Ctr, Dallas, TX USA Columbia Univ, Med Ctr, New York, NY USAKubanek, Milos论文数: 0 引用数: 0 h-index: 0机构: Inst Clin & Expt Med, Prague 4, Czech Republic Columbia Univ, Med Ctr, New York, NY USAPoulsen, Steen论文数: 0 引用数: 0 h-index: 0机构: Aarhus Univ Hosp, Aarhus N, Denmark Columbia Univ, Med Ctr, New York, NY USADamy, Thibaud论文数: 0 引用数: 0 h-index: 0机构: Hop Henri Mondor, Creteil, France Columbia Univ, Med Ctr, New York, NY USA论文数: 引用数: h-index:机构:Tahara, Nobuhiro论文数: 0 引用数: 0 h-index: 0机构: Kurume Univ Hosp, Kurume, Japan Columbia Univ, Med Ctr, New York, NY USAYu, Wen-Chung论文数: 0 引用数: 0 h-index: 0机构: Taipei Vet Gen Hosp, Taipei, Taiwan Columbia Univ, Med Ctr, New York, NY USATang, W. H. Wilson论文数: 0 引用数: 0 h-index: 0机构: Heart Vasc & Thorac Inst, Cleveland, OH USA Columbia Univ, Med Ctr, New York, NY USAObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn Irccs Policlin San Matteo Pavia, Pavia, Italy Columbia Univ, Med Ctr, New York, NY USAGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med Nutr & Salvador Zubiran, Mexico City, DF, Mexico Columbia Univ, Med Ctr, New York, NY USASekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ Hosp, Matsumoto, Japan Columbia Univ, Med Ctr, New York, NY USAWhite, Matthew T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAJay, Patrick Y.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Wayland, MA USA Columbia Univ, Med Ctr, New York, NY USAVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnlyam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: Natl Amyloidosis Ctr, London, England Columbia Univ, Med Ctr, New York, NY USA
- [18] PRIMARY RESULTS FROM APOLLO-B, A PHASE 3 STUDY OF PATISIRAN IN PATIENTS WITH TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHYEUROPEAN HEART JOURNAL SUPPLEMENTS, 2023, 25 : D28 - D28Longhi, S.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyMaurer, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyFontana, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyBerk, J.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyGustafsson, F.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalySimoes, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyGrogan, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyFernandes, F.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyGottlieb, R.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyKubanek, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyPoulsen, S.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyDamy, T.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyDiemberger, I.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyTahara, N.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyYu, W.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyTang, W.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyObici, L.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyGonzalez-Duarte, A.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalySekijima, Y.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyWhite, M.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyYureneva, E.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyJay, P.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyVest, J.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, ItalyGillmore, J.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Azienda Osped Univ Bologna, Cardiac Thorac & Vasc Dept, Cardiol Unit, Bologna, Italy
- [19] PRIMARY RESULTS FROM APOLLO-B, A PHASE 3 STUDY OF PATISIRAN IN PATIENTS WITH TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHYEUROPEAN HEART JOURNAL SUPPLEMENTS, 2022, 24Longhi, Simone论文数: 0 引用数: 0 h-index: 0机构: Irccs Aou Bologna, Div Cardiol, Bologna, Italy Columbia Univ, Med Ctr, New York, NY USAMaurer, Mathew S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Med Ctr, New York, NY USA Columbia Univ, Med Ctr, New York, NY USAFontana, Marianna论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Div Med, London, England Columbia Univ, Med Ctr, New York, NY USABerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Sch Med, Boston, MA USA Columbia Univ, Med Ctr, New York, NY USAGustafsson, Finn论文数: 0 引用数: 0 h-index: 0机构: Copenhagen Univ Hosp, Dept Cardiol, Copenhagen, Denmark Columbia Univ, Med Ctr, New York, NY USASimoes, Marcos论文数: 0 引用数: 0 h-index: 0机构: Univ Sao Paulo, Fac Med Ribeirao Preto, Hosp Clin, Upc, Sao Paulo, Brazil Columbia Univ, Med Ctr, New York, NY USAGrogan, Martha论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Coll Med, Div Cardiovasc Dis, Rochester, MN USA Columbia Univ, Med Ctr, New York, NY USAFernandes, Fabio论文数: 0 引用数: 0 h-index: 0机构: Hcfmusp, Inst Coracao, Sao Paulo, Brazil Columbia Univ, Med Ctr, New York, NY USAGottlieb, Robert L.论文数: 0 引用数: 0 h-index: 0机构: Baylor Univ, Med Ctr, Ctr Adv Heart & Lung Dis, Dallas, TX USA Columbia Univ, Med Ctr, New York, NY USAKubanek, Milos论文数: 0 引用数: 0 h-index: 0机构: Inst Klin & Expt Med, Prague, Czech Republic Columbia Univ, Med Ctr, New York, NY USAPoulsen, Steen论文数: 0 引用数: 0 h-index: 0机构: Aarhus Univ Hosp, Aarhus, Denmark Columbia Univ, Med Ctr, New York, NY USADamy, Thibaud论文数: 0 引用数: 0 h-index: 0机构: Hop Henri Mondor, Creteil, France Columbia Univ, Med Ctr, New York, NY USA论文数: 引用数: h-index:机构:Tahara, Nobuhiro论文数: 0 引用数: 0 h-index: 0机构: Kurume Univ Hosp, Kurume, Fukuoka, Japan Columbia Univ, Med Ctr, New York, NY USAYu, Wen-chuhg论文数: 0 引用数: 0 h-index: 0机构: Taipei Vet Gen Hosp, Taipei, Taiwan Columbia Univ, Med Ctr, New York, NY USATang, W. H. Wilson论文数: 0 引用数: 0 h-index: 0机构: Cleveland Clin, Heart Vasc & Thorac Inst, Cleveland, OH USA Columbia Univ, Med Ctr, New York, NY USAObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn Irccs Policlin San Matteo Pavia, Amyloidosis Res & Treatment Ctr, Pavia, Italy Columbia Univ, Med Ctr, New York, NY USAGonzalez-duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Columbia Univ, Med Ctr, New York, NY USASekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ Hosp, Matsumoto, Nagano, Japan Columbia Univ, Med Ctr, New York, NY USAWhite, Matthew T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAYureneva, Elena论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAJay, Patrick Y.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Columbia Univ, Med Ctr, New York, NY USAGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: Royal Free Hosp, UCL Med Sch, Natl Amyloidosis Ctr, London, England Columbia Univ, Med Ctr, New York, NY USA
- [20] A retrospective survey of patients with hereditary transthyretin-mediated (hATTR) amyloidosis treated with patisiran in real-world clinical practice in BelgiumACTA NEUROLOGICA BELGICA, 2023, 123 (03) : 1029 - 1037De Bleecker, Jan L.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Ghent, Dept Neurol, Ghent, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumClaeys, Kristl G.论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, Dept Neurol, Univ Hosp Leuven, Lab Muscle Dis & Neuropathies, Leuven, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumDelstanche, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Liege, Dept Neurol, Liege, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumVan Parys, Vinciane论文数: 0 引用数: 0 h-index: 0机构: Clin Univ St Luc, Dept Neurol, Brussels, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumBaets, Jonathan论文数: 0 引用数: 0 h-index: 0机构: UAntwerpen, Dept Neurol, Antwerp Univ Hosp, Fac Med & Hlth Sci,Translat Neurosci, Antwerp, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumTilleux, Sebastien论文数: 0 引用数: 0 h-index: 0机构: Alnylam Belgium BVBA, Schumanpl 6, B-1040 Brussels, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, BelgiumRemiche, Gauthier论文数: 0 引用数: 0 h-index: 0机构: Univ Libre Bruxelles ULB, Hop Erasme, Dept Neurol, Brussels, Belgium Univ Hosp Ghent, Dept Neurol, Ghent, Belgium