Safety and Increased Transduction Efficiency in the Adult Nonhuman Primate Central Nervous System with Intravenous Delivery of Two Novel Adeno-Associated Virus Capsids

被引：0
|
作者：
Sah, Dinah [1 ]
Mazzarelli, Allyse [1 ]
Christensen, Emily [1 ]
Thompson, Jeff [1 ]
Lindgren, Holly [1 ]
Felix-Ortiz, Ada [1 ]
Aubin, Justin [1 ]
Scheel, Maria [1 ]
Pechan, Peter [1 ]
Horowitz, Eric [1 ]
Fine, Shamone [1 ]
Shu, Yanqun [1 ]
Zhou, Xiaochuan [1 ]
Gamba-Vitalo, Christina [1 ]
Carter, Todd [1 ]
Chen, Qingmin [1 ]
Carroll, Jenna [1 ]
Goulet, Martin [1 ]
Patzke, Holger [1 ]
机构：
[1] Voyager Therapeut, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
661
引用
收藏
页码：305 / 305
页数：1
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