Safety and Increased Transduction Efficiency in the Adult Nonhuman Primate Central Nervous System with Intravenous Delivery of Two Novel Adeno-Associated Virus Capsids

被引：0

作者：

Sah, Dinah ^{[1
]}

Mazzarelli, Allyse ^{[1
]}

Christensen, Emily ^{[1
]}

Thompson, Jeff ^{[1
]}

Lindgren, Holly ^{[1
]}

Felix-Ortiz, Ada ^{[1
]}

Aubin, Justin ^{[1
]}

Scheel, Maria ^{[1
]}

Pechan, Peter ^{[1
]}

Horowitz, Eric ^{[1
]}

Fine, Shamone ^{[1
]}

Shu, Yanqun ^{[1
]}

Zhou, Xiaochuan ^{[1
]}

Gamba-Vitalo, Christina ^{[1
]}

Carter, Todd ^{[1
]}

Chen, Qingmin ^{[1
]}

Carroll, Jenna ^{[1
]}

Goulet, Martin ^{[1
]}

Patzke, Holger ^{[1
]}

机构：

[1] Voyager Therapeut, Cambridge, MA USA

来源：

MOLECULAR THERAPY | 2018年 / 26卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

661

引用

页码：305 / 305

页数：1

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