Safety and Increased Transduction Efficiency in the Adult Nonhuman Primate Central Nervous System with Intravenous Delivery of Two Novel Adeno-Associated Virus Capsids

被引:0
|
作者
Sah, Dinah [1 ]
Mazzarelli, Allyse [1 ]
Christensen, Emily [1 ]
Thompson, Jeff [1 ]
Lindgren, Holly [1 ]
Felix-Ortiz, Ada [1 ]
Aubin, Justin [1 ]
Scheel, Maria [1 ]
Pechan, Peter [1 ]
Horowitz, Eric [1 ]
Fine, Shamone [1 ]
Shu, Yanqun [1 ]
Zhou, Xiaochuan [1 ]
Gamba-Vitalo, Christina [1 ]
Carter, Todd [1 ]
Chen, Qingmin [1 ]
Carroll, Jenna [1 ]
Goulet, Martin [1 ]
Patzke, Holger [1 ]
机构
[1] Voyager Therapeut, Cambridge, MA USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
661
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收藏
页码:305 / 305
页数:1
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