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- [43] Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosis AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2024, 31 : S68 - S68
- [48] Impact of Patisiran, an RNAi Therapeutic, on Diarrhea Symptoms in Patients With Hereditary Transthyretin-Mediated Amyloidosis AMERICAN JOURNAL OF GASTROENTEROLOGY, 2020, 115 : S1657 - S1657