Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosis

被引：0
|
作者：
Wixner, Jonas [1 ,2 ]
Conceicao, Isabel [3 ]
Berk, John [4 ]
Adams, David [5 ]
Polydefkis, Michael [6 ]
Shahram, Attarian [7 ]
Gillmore, Julian D. [8 ,9 ]
Dyck, P. James B. [10 ]
Coelho, Teresa [11 ]
Chen, Jersey [12 ]
Hardy, Elise [12 ]
Kwoh, Jesse [13 ]
Natman, Jonatan [12 ]
Cruz, Marcia Waddington [13 ]
机构：
[1] Umea Univ, Umea, Sweden
[2] Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden
[3] Governo Republ Portuguesa, Lisbon, Portugal
[4] Boston Univ, Boston, MA USA
[5] Republ Francaise, Paris, France
[6] Johns Hopkins Univ, Baltimore, MD USA
[7] Timone Univ Hosp, Referral Ctr Neuromuscular Dis & ALS, APHM, Marseille, France
[8] Euro NMD, Filnemus, Marseille, France
[9] Univ London, London, England
[10] Mayo Fdn Med Educ & Res, Rochester, MN USA
[11] Ctr Hosp Univ Santo Antonio, Unidade Corino Andrade, Porto, Portugal
[12] AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA
[13] Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA
来源：
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS | 2024年 / 31卷
关键词：
D O I：
暂无
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
174
引用
收藏
页码：S68 / S68
页数：1
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