Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosis

被引：0

作者：

Wixner, Jonas ^{[1
,2
]}

Conceicao, Isabel ^{[3
]}

Berk, John ^{[4
]}

Adams, David ^{[5
]}

Polydefkis, Michael ^{[6
]}

Shahram, Attarian ^{[7
]}

Gillmore, Julian D. ^{[8
,9
]}

Dyck, P. James B. ^{[10
]}

Coelho, Teresa ^{[11
]}

Chen, Jersey ^{[12
]}

Hardy, Elise ^{[12
]}

Kwoh, Jesse ^{[13
]}

Natman, Jonatan ^{[12
]}

Cruz, Marcia Waddington ^{[13
]}

机构：

[1] Umea Univ, Umea, Sweden

[2] Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden

[3] Governo Republ Portuguesa, Lisbon, Portugal

[4] Boston Univ, Boston, MA USA

[5] Republ Francaise, Paris, France

[6] Johns Hopkins Univ, Baltimore, MD USA

[7] Timone Univ Hosp, Referral Ctr Neuromuscular Dis & ALS, APHM, Marseille, France

[8] Euro NMD, Filnemus, Marseille, France

[9] Univ London, London, England

[10] Mayo Fdn Med Educ & Res, Rochester, MN USA

[11] Ctr Hosp Univ Santo Antonio, Unidade Corino Andrade, Porto, Portugal

[12] AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA

[13] Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA

来源：

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS | 2024年 / 31卷

关键词：

D O I：

暂无

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

174

引用

页码：S68 / S68

页数：1

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