Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosis

被引：0

作者：

Wixner, Jonas ^{[1
,2
]}

Conceicao, Isabel ^{[3
]}

Berk, John ^{[4
]}

Adams, David ^{[5
]}

Polydefkis, Michael ^{[6
]}

Shahram, Attarian ^{[7
]}

Gillmore, Julian D. ^{[8
,9
]}

Dyck, P. James B. ^{[10
]}

Coelho, Teresa ^{[11
]}

Chen, Jersey ^{[12
]}

Hardy, Elise ^{[12
]}

Kwoh, Jesse ^{[13
]}

Natman, Jonatan ^{[12
]}

Cruz, Marcia Waddington ^{[13
]}

机构：

[1] Umea Univ, Umea, Sweden

[2] Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden

[3] Governo Republ Portuguesa, Lisbon, Portugal

[4] Boston Univ, Boston, MA USA

[5] Republ Francaise, Paris, France

[6] Johns Hopkins Univ, Baltimore, MD USA

[7] Timone Univ Hosp, Referral Ctr Neuromuscular Dis & ALS, APHM, Marseille, France

[8] Euro NMD, Filnemus, Marseille, France

[9] Univ London, London, England

[10] Mayo Fdn Med Educ & Res, Rochester, MN USA

[11] Ctr Hosp Univ Santo Antonio, Unidade Corino Andrade, Porto, Portugal

[12] AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA

[13] Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA

来源：

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS | 2024年 / 31卷

关键词：

D O I：

暂无

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

174

引用

页码：S68 / S68

页数：1

共 50 条

[41] Kidney Function And Proteinuria With Eplontersen Treatment For Hereditary Transthyretin Amyloidosis
Maurer, Mathew s
Gillmore, Julian D.
Berk, John l
Masri, Ahmad
DA Silva, Moises dias
Kwoh, Jesse
Littl, Dustin j
Natman, Jonatan
Zhou, Wunan
Waddington-cruz, Marcia
JOURNAL OF CARDIAC FAILURE, 2025, 31 (01) : 346 - 347
[42] IDENTIFYING MIXED PHENOTYPE: EVALUATING THE PRESENCE OF POLYNEUROPATHY IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH CARDIOMYOPATHY
Grogan, Martha
Hawkins, Philip
Kristen, Arnt
Berk, John
Suhr, Ole B.
Lin, Hollis
Merkel, Madeline
McManus, Anastasia
Powell, Christine
Vest, John
Karsten, Verena
Judge, Daniel
MUSCLE & NERVE, 2020, 62 : S107 - S107
[43] Identifying Mixed Phenotype: Evaluating the Presence of Polyneuropathy in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Cardiomyopathy
Merkel, Madeline
Grogan, Martha
Hawkins, Philip N.
Kristen, Arnt V.
Berk, John L.
Suhr, Ole B.
Lin, Hollis
McManus, Anastasia
Powell, Christine
Vest, John
Karsten, Verena
Judge, Daniel P.
NEUROLOGY, 2020, 94 (15)
[44] Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial
Adams, David
Tournev, Ivailo L.
Taylor, Mark S.
Coelho, Teresa
Plante-Bordeneuve, Violaine
Berk, John L.
Gonzalez-Duarte, Alejandra
Gillmore, Julian D.
Low, Soon-Chai
Sekijima, Yoshiki
Obici, Laura
Chen, Chongshu
Badri, Prajakta
Arum, Seth M.
Vest, John
Polydefkis, Michael
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2023, 30 (01): : 18 - 26
[45] Long-term integrated safety of patisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
Gillmore, J.
Berk, J.
Dispenzieri, A.
Polydefkis, M.
Gonzalez-Duarte, A.
Sekijima, Y.
Sweetser, M. T.
Arum, S.
Wang, J. J.
White, M. T.
Maurer, M.
EUROPEAN HEART JOURNAL, 2020, 41 : 2129 - 2129
[46] Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
Laura Obici
Senda Ajroud-Driss
Kon-Ping Lin
John L. Berk
Julian D. Gillmore
Parag Kale
Haruki Koike
David Danese
Emre Aldinc
Chongshu Chen
John Vest
David Adams
Neurology and Therapy, 2023, 12 (5) : 1759 - 1775
[47] Pharmacokinetics of Patisiran, the First Approved RNA Interference Therapy in Patients With Hereditary Transthyretin-Mediated Amyloidosis
Zhang, Xiaoping
Goel, Varun
Robbie, Gabriel J.
JOURNAL OF CLINICAL PHARMACOLOGY, 2020, 60 (05): : 573 - 585
[48] Impact of vutrisiran on exploratory cardiac parameters in hereditary transthyretin-mediated amyloidosis with polyneuropathy
Garcia-Pavia, Pablo
Grogan, Martha
Kale, Parag
Berk, John L.
Maurer, Mathew S.
Conceicao, Isabel
Di Carli, Marcelo
Solomon, Scott D.
Chen, Chongshu
Yureneva, Elena
Vest, John
Gillmore, Julian D.
EUROPEAN JOURNAL OF HEART FAILURE, 2024, 26 (02) : 397 - 410
[49] Practical Guidance for the Use of Patisiran in the Management of Polyneuropathy in Hereditary Transthyretin-Mediated Amyloidosis
Dixon, Stacy
Kang, Xuan
Quan, Dianna
THERAPEUTICS AND CLINICAL RISK MANAGEMENT, 2023, 19 : 973 - 981
[50] Treatment with patisiran of a patient with hereditary transthyretin-mediated amyloidosis with stage 3 polyneuropathy
Mueschen, Lars H.
Koerner, Gudrun
Gingele, Stefan
Haenselmann, Anja
Bavendiek, Udo
Skripuletz, Thomas
MUSCLE & NERVE, 2021, 64 (03) : E11 - E13

← 1 2 3 4 5 →