Initial therapeutic response to enzyme replacement therapy with Myozyme® in a sibling cohort with late-onset Pompe disease

被引：0

作者：

Hughes, D. S. ^{[1
]}

Norwood, F. ^{[2
]}

Sawicka, E. ^{[3
]}

Milligan, A. ^{[1
]}

Pringle, S. ^{[1
]}

Bruce, R. ^{[1
]}

Goodwin, S. ^{[1
]}

Jennings, A. ^{[1
]}

Richfield, L. ^{[1
]}

Mehta, A. B. ^{[1
]}

机构：

[1] UCL Royal Free & Univ Coll Med Sch, Lysosomal Storage Disorders Unit, London WC1E 6BT, England

[2] Kings Coll Hosp London, Dept Neurol, London, England

[3] Princess Royal Univ Hosp, Dept Thorac Med, Kent, England

来源：

CLINICAL THERAPEUTICS | 2008年 / 30卷

关键词：

D O I：

暂无

中图分类号：

R9 [药学];

学科分类号：

1007 ;

摘要：

引用

页码：S29 / S30

页数：2

共 50 条

[41] Functional capacity in a late-onset Pompe disease patient: Effect of enzyme replacement therapy and exercise training
Krase, Argyro A.
Papadimas, Giorgos K.
Terzis, Gerasimos D.
ANNALS OF INDIAN ACADEMY OF NEUROLOGY, 2016, 19 (03) : 423 - U136
[42] Early signs of benefit in a child with late-onset Pompe disease after treatment with enzyme replacement therapy
Lianou, D.
Syrengelas, D.
Poulopoulos, P.
Klimentopoulou, A.
Mavridou, I.
Michelakakis, H.
CLINICAL THERAPEUTICS, 2007, 29 : S121 - S121
[43] Enzyme replacement therapy induces T-cell responses in late-onset Pompe's disease
Banati, M.
Hosszu, Z.
Trauninger, A.
Szereday, L.
Illes, Z.
JOURNAL OF NEUROLOGY, 2011, 258 : 253 - 253
[44] Hypersensitivity infusion-associated reactions induced by enzyme replacement therapy in a cohort of patients with late-onset Pompe disease: An experience from the French Pompe Registry
Lessard, Lola E. R.
Tard, Celine
Salort-Campana, Emmanuelle
Sacconi, Sabrina
Behin, Anthony
Bassez, Guillaume
Orlikowski, David
Merle, Philippe
Nollet, Sylvain
Gallay, Laure
Berard, Frederic
Robinson, Philip
Bouhour, Francoise
Laforet, Pascal
MOLECULAR GENETICS AND METABOLISM, 2023, 139 (03)
[45] Enzyme replacement therapy in late-onset Pompe's disease: A three-year follow-up
Winkel, LPF
Van den Hout, JMP
Kamphoven, JHJ
Disseldorp, JAM
Remmerswaal, M
Arts, WFM
Loonen, MCB
Vulto, AG
Van Doorn, PA
De Jong, G
Hop, W
Smit, GPA
Shapira, SK
Boer, MA
van Diggelen, OP
Reuser, AJJ
Van der Ploeg, AT
ANNALS OF NEUROLOGY, 2004, 55 (04) : 495 - 502
[46] Effect of aerobic and resistance exercise training on late-onset Pompe disease patients receiving enzyme replacement therapy
Terzis, Gerasimos
Dimopoulos, Filippos
Papadimas, George K.
Papadopoulos, Constantinos
Spengos, Konstantinos
Fatouros, Ioannis
Kavouras, Stavros A.
Manta, Panagiota
MOLECULAR GENETICS AND METABOLISM, 2011, 104 (03) : 279 - 283
[47] Effect of Aerobic and Resistance Exercise Training on Late-Onset Pompe Disease Patients Receiving Enzyme Replacement Therapy
Terzis, Gerasimos
Papadimas, Georgios K.
Dimopoulos, Filippos
Papadopoulos, Costas
Spengos, Konstantinos
Fatouros, Ioannis
Kavouras, Stavros
Manta, Panagiota
CLINICAL THERAPEUTICS, 2011, 33 : S40 - S40
[48] Long-term enzyme replacement therapy with alglucosidase alfa in children and adults with late-onset Pompe disease
Theunissen, M.
van Kooten, H.
Harlaar, L.
Ismailova, G.
van den Hout, J.
Rizopoulos, D.
Boon, M.
Brusse, E.
van Doorn, P.
van der Ploeg, A.
van der Beek, N.
NEUROMUSCULAR DISORDERS, 2023, 33 : S150 - S150
[49] Effects of exercise training during infusion on late-onset Pompe disease patients receiving enzyme replacement therapy
Terzis, Gerasimos
Krase, Argyro
Papadimas, Giorgos
Papadopoulos, Constantinos
Kavouras, Stavros A.
Manta, Panagiota
MOLECULAR GENETICS AND METABOLISM, 2012, 107 (04) : 669 - 673
[50] Improvement of bone mineral density after enzyme replacement therapy in Chinese late-onset Pompe disease patients
Sheng B.
Chu Y.P.
Wong W.T.
Yau E.K.C.
Chen S.P.L.
Luk W.H.
BMC Research Notes, 10 (1)

← 1 2 3 4 5 →