Initial therapeutic response to enzyme replacement therapy with Myozyme® in a sibling cohort with late-onset Pompe disease

被引：0
|
作者：
Hughes, D. S. [1 ]
Norwood, F. [2 ]
Sawicka, E. [3 ]
Milligan, A. [1 ]
Pringle, S. [1 ]
Bruce, R. [1 ]
Goodwin, S. [1 ]
Jennings, A. [1 ]
Richfield, L. [1 ]
Mehta, A. B. [1 ]
机构：
[1] UCL Royal Free & Univ Coll Med Sch, Lysosomal Storage Disorders Unit, London WC1E 6BT, England
[2] Kings Coll Hosp London, Dept Neurol, London, England
[3] Princess Royal Univ Hosp, Dept Thorac Med, Kent, England
来源：
CLINICAL THERAPEUTICS | 2008年 / 30卷
关键词：
D O I：
暂无
中图分类号：
R9 [药学];
学科分类号：
1007 ;
摘要：
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收藏
页码：S29 / S30
页数：2
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