Muscle-targeted gene therapy in glycogen storage disease type II with adeno-associated virus serotypes 7, 8, and 9

被引：0
|
作者：
Sun, Baodong [1 ]
Hauschka, Stephen [2 ]
Bird, Andrew [1 ]
Auten, Richard [3 ]
Koeberl, Divight [1 ]
机构：
[1] Duke Univ, Med Ctr, Dept Pediat, Div Med Genet, Durham, NC 27706 USA
[2] Univ Washington, Dept Biochem, Seattle, WA 98195 USA
[3] Duke Univ, Med Ctr, Dept Pediat, Div Neonatol, Durham, NC 27706 USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2008年 / 93卷 / 02期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
95
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收藏
页码：S38 / S39
页数：2
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