共 50 条
- [21] Recombinant adeno-associated virus for muscle directed gene therapyNature Medicine, 1997, 3 : 306 - 312Krishna J. Fisher论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Karin Jooss论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,James Alston论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Yiping Yang论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Sarah Ehlen Haecker论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Katherine High论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Ravindra Pathak论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,Steven E. Raper论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,James M. Wilson论文数: 0 引用数: 0 h-index: 0机构: Institute for Human Gene Therapy and Departments of Medicine and Molecular and Cellular Engineering,
- [22] Development of adeno-associated virus (AAV) vectors for gene therapy in the mouse model for glycogen storage disease type Ia (GSD-Ia)MOLECULAR THERAPY, 2004, 9 : S404 - S404Koeberl, DD论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USASun, BD论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USAFranco, L论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USABird, A论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USAFaulkner, E论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USAChen, YT论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA Duke Univ, Med Ctr, Div Med Genet, Durham, NC USA
- [23] Sustained correction of glycogen storage disease type II by recombinant adeno-associated virus serotype 1 (AAV1) vector-mediated gene therapyCIRCULATION, 2004, 110 (17) : 160 - 160Mah, C论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USACresawn, K论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAFraites, TJ论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAPacak, CA论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USALewis, MA论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USABynre, BJ论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USA
- [24] Adeno-Associated Virus-Mediated Correction of a Canine Model of Glycogen Storage Disease Type IaHUMAN GENE THERAPY, 2010, 21 (07) : 903 - 910Weinstein, David A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USACorreia, Catherine E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAConlon, Thomas论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USASpecht, Andrew论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Small Anim Med, Dept Small Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAVerstegen, John论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Theriogenol, Dept Large Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAOnclin-Verstegen, Karine论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Theriogenol, Dept Large Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USACampbell-Thompson, Martha论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pathol Immunol & Lab Med, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USADhaliwal, Gurmeet论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Theriogenol, Dept Large Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAMirian, Layla论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Div Theriogenol, Dept Large Anim Clin Sci, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USACossette, Holly论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAFalk, Darin J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAGermain, Sean论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAClement, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAPorvasnik, Stacy论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAFiske, Laurie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAStruck, Maggie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Anim Care Serv, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USARamirez, Harvey E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Anim Care Serv, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAJordan, Juan论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Anim Care Serv, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAAndrutis, Karl论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Anim Care Serv, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAChou, Janice Y.论文数: 0 引用数: 0 h-index: 0机构: NICHHD, Sect Cellular Differentiat, Program Dev Endocrinol & Genet, NIH, Bethesda, MD 20892 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAByrne, Barry J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Div Cellular & Mol Therapy, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USAMah, Cathryn S.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, Div Cellular & Mol Therapy, Dept Pediat, Gainesville, FL 32610 USA Univ Florida, Coll Med, Glycogen Storage Dis Program, Div Pediat Endocrinol,Dept Pediat, Gainesville, FL 32610 USA
- [25] Adeno-associated virus (AAV) gene therapy for neurological diseaseNEUROPHARMACOLOGY, 2013, 69 : 82 - 88Weinberg, Marc S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Dept Pharmacol, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USAMcCown, Thomas J.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Dept Psychiat, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA
- [26] Structural Studies of Adeno-Associated Virus Serotypes towards Improved Gene Therapy ApplicationsMOLECULAR THERAPY, 2009, 17 : S144 - S145Agbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAGovindasamy, Lakshmanan论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USANam, Hyun-Joo论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAGurda, Brittney论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USANg, Robert论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAMcKenna, Robert论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAZolotukhin, Sergei论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAMuzyczka, Nicholas论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAOlson, Norm论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA 92103 USA Univ Florida, Gainesville, FL USABaker, Timothy论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA 92103 USA Univ Florida, Gainesville, FL USAChiorini, John A.论文数: 0 引用数: 0 h-index: 0机构: NIDCR, GTTB, NIH, Bethesda, MD USA Univ Florida, Gainesville, FL USAKozyreva, Olga论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ Florida, Gainesville, FL USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ Florida, Gainesville, FL USA
- [27] Structure of adeno-associated virus serotype 8, a gene therapy vectorJOURNAL OF VIROLOGY, 2007, 81 (22) : 12260 - 12271Nam, Hyun-Joo论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USALane, Michael Douglas论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAPadron, Eric论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAGurda, Brittney论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA论文数: 引用数: h-index:机构:Kohlbrenner, Erik论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAAslanidi, George论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAByrne, Barry论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA Univ Florida, Coll Med, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAMuzyczka, Nicholas论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL 32610 USA Univ Florida, Coll Med, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAZolotukhin, Sergei论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA Univ Florida, McKnight Brain Inst, Struct Biol Ctr, Dept Biochem & Mol Biol,Coll Med, Gainesville, FL 32610 USA
- [28] Differential myofiber-type transduction preference of adeno-associated virus serotypes 6 and 9Skeletal Muscle, 5Muhammad Riaz论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsYotam Raz论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsElizabeth B. Moloney论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsMaaike van Putten论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsYvonne D. Krom论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsSilvere M. van der Maarel论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsJoost Verhaagen论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human GeneticsVered Raz论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Department of Human Genetics
- [29] Generation of Targeted Adeno-Associated Virus (AAV) Vectors for Human Gene TherapyCURRENT PHARMACEUTICAL DESIGN, 2015, 21 (22) : 3248 - 3256Liu, Yarong论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USA Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USASiriwon, Natnaree论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USA Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USARohrs, Jennifer A.论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Dept Biomed Engn, Los Angeles, CA 90089 USA Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USAWang, Pin论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USA Univ So Calif, Dept Biomed Engn, Los Angeles, CA 90089 USA Univ So Calif, Dept Pharmacol & Pharmaceut Sci, Los Angeles, CA 90089 USA Univ So Calif, Mork Family Dept Chem Engn & Mat Sci, Los Angeles, CA 90089 USA
- [30] Adeno Associated Vector-Based Gene Therapy for Glycogen Storage Disease Type 3MOLECULAR THERAPY, 2019, 27 (04) : 244 - 245Vidal, Patrice论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France INSERM, U951, Evry, France Genethon, IMF, Evry, FranceJauze, Louisa论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France INSERM, U951, Evry, France Genethon, IMF, Evry, FranceLe Brun, Pierre-Romain论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France INSERM, U951, Evry, France Genethon, IMF, Evry, FranceColella, Pasqualina论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France INSERM, U951, Evry, France Genethon, IMF, Evry, FranceCharles, Severine论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceCollaud, Fanny论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceDaniele, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceVan Wittenberghe, Laetitia论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceGjata, Bernard论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceLaforet, Pascal论文数: 0 引用数: 0 h-index: 0机构: Hop Raymond Poincare, Garches, France Genethon, IMF, Evry, FranceMalfatti, Eduardo论文数: 0 引用数: 0 h-index: 0机构: La Pitie Salpetriere Hosp, Paris, France Genethon, IMF, Evry, FranceMingozzi, Federico论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, FranceRonzitti, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: Genethon, IMF, Evry, France Genethon, IMF, Evry, France