Muscle-targeted gene therapy in glycogen storage disease type II with adeno-associated virus serotypes 7, 8, and 9

被引:0
|
作者
Sun, Baodong [1 ]
Hauschka, Stephen [2 ]
Bird, Andrew [1 ]
Auten, Richard [3 ]
Koeberl, Divight [1 ]
机构
[1] Duke Univ, Med Ctr, Dept Pediat, Div Med Genet, Durham, NC 27706 USA
[2] Univ Washington, Dept Biochem, Seattle, WA 98195 USA
[3] Duke Univ, Med Ctr, Dept Pediat, Div Neonatol, Durham, NC 27706 USA
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中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
95
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页码:S38 / S39
页数:2
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