Patient-specific iPSC-derived endothelial cells provide longterm phenotypic correction of hemophilia A

被引：0

作者：

Olgasi, C. ^{[1
]}

Talmon, M. ^{[1
]}

Merlin, S. ^{[1
]}

Cucci, A. ^{[1
]}

Richaud-Patin, Y. ^{[2
,3
]}

Colangelo, D. ^{[1
]}

di Scipio, F. ^{[4
]}

Berta, G. N. ^{[4
]}

Borsotti, C. ^{[1
]}

Valeri, F. ^{[5
]}

Lombardo, A. ^{[6
,7
,8
]}

Raya, A. ^{[2
,3
,9
]}

Follenzi, A. ^{[1
]}

机构：

[1] Univ Piemonte Orientale, Dept Hlth Sci, Novara, Italy

[2] Hosp Durans Reynals, Ctr Regenerat Med Barcelona CMRB, Lhospitalet De Llobregat, Barcelona, Spain

[3] Ctr Networked Biomed Res Bioengn Biomat & Nanomed, Madrid 28029, Spain

[4] Azienda Osp Univ San Luigi Gonzaga, Orbassano, Italy

[5] AOU Citta Salute & Sci, Turin, Italy

[6] San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy

[7] Ist Sci San Raffaele, Milan, Italy

[8] Univ Vita Salute San Raffaele, Milan, Italy

[9] Inst Catalana Recerca & Estudis Avancats ICREA, Barcelona 08010, Spain

来源：

HUMAN GENE THERAPY | 2018年 / 29卷 / 12期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P171

引用

页码：A78 / A78

页数：1

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