Patient-specific iPSC-derived endothelial cells provide longterm phenotypic correction of hemophilia A

被引：0
|
作者：
Olgasi, C. [1 ]
Talmon, M. [1 ]
Merlin, S. [1 ]
Cucci, A. [1 ]
Richaud-Patin, Y. [2 ,3 ]
Colangelo, D. [1 ]
di Scipio, F. [4 ]
Berta, G. N. [4 ]
Borsotti, C. [1 ]
Valeri, F. [5 ]
Lombardo, A. [6 ,7 ,8 ]
Raya, A. [2 ,3 ,9 ]
Follenzi, A. [1 ]
机构：
[1] Univ Piemonte Orientale, Dept Hlth Sci, Novara, Italy
[2] Hosp Durans Reynals, Ctr Regenerat Med Barcelona CMRB, Lhospitalet De Llobregat, Barcelona, Spain
[3] Ctr Networked Biomed Res Bioengn Biomat & Nanomed, Madrid 28029, Spain
[4] Azienda Osp Univ San Luigi Gonzaga, Orbassano, Italy
[5] AOU Citta Salute & Sci, Turin, Italy
[6] San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy
[7] Ist Sci San Raffaele, Milan, Italy
[8] Univ Vita Salute San Raffaele, Milan, Italy
[9] Inst Catalana Recerca & Estudis Avancats ICREA, Barcelona 08010, Spain
来源：
HUMAN GENE THERAPY | 2018年 / 29卷 / 12期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P171
引用
收藏
页码：A78 / A78
页数：1
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