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- [1] Patient-Specific iPSC-Derived RPE for Modeling of Retinal DiseasesJOURNAL OF CLINICAL MEDICINE, 2015, 4 (04): : 567 - 578Nguyen, Huy V.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Coll Phys & Surg, 100 Haven Ave,Apt 14B, New York, NY 10032 USA Columbia Univ, Coll Phys & Surg, 100 Haven Ave,Apt 14B, New York, NY 10032 USALi, Yao论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Ophthalmol, New York, NY 10032 USA Columbia Univ, Coll Phys & Surg, 100 Haven Ave,Apt 14B, New York, NY 10032 USATsang, Stephen H.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Ophthalmol, New York, NY 10032 USA Columbia Univ, Coll Phys & Surg, 100 Haven Ave,Apt 14B, New York, NY 10032 USA
- [2] Decreased phagocytosis of photoreceptor outer segments in patient-specific iPSC-derived RPE on diseased basement membraneINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2020, 61 (07)Gong, Jie论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Ophthalmol, New Haven, CT USA Yale Univ, Ophthalmol, New Haven, CT USACai, Huey论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Ophthalmol, New Haven, CT USA Yale Univ, Ophthalmol, New Haven, CT USARizzolo, Lawrence J.论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Ophthalmol, New Haven, CT USA Yale Univ, Ophthalmol, New Haven, CT USAFields, Mark Anthony论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Ophthalmol, New Haven, CT USA Yale Univ, Ophthalmol, New Haven, CT USADel Priore, Lucian V.论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Ophthalmol, New Haven, CT USA Yale Univ, Ophthalmol, New Haven, CT USA
- [3] Patient-specific iPSC-derived cellular models of LGMDR1STEM CELL RESEARCH, 2021, 53Mateos-Aierdi, A. J.论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainDehesa-Etxebeste, M.论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainGoicoechea, M.论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainAiastui, A.论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainRichaud-Patin, Y.论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Biomed Res Inst IDIBELL, Program Regenerat Med, Lhospitalet De Llobregat, Spain Inst Salud Carlos III, CIBER BBN, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainJimenez-Delgado, S.论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Biomed Res Inst IDIBELL, Program Regenerat Med, Lhospitalet De Llobregat, Spain Inst Salud Carlos III, CIBER BBN, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainRaya, A.论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Biomed Res Inst IDIBELL, Program Regenerat Med, Lhospitalet De Llobregat, Spain Inst Salud Carlos III, CIBER BBN, Madrid, Spain ICREA, Barcelona, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, SpainNaldaiz-Gastesi, N.论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, Spainde Munain, A. Lopez论文数: 0 引用数: 0 h-index: 0机构: Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain Inst Salud Carlos III, CIBERNED, Madrid, Spain Univ Basque Country, Dept Neurosci, San Sebastian, Spain Hosp Univ Donostia, Dept Neurol, San Sebastian, Spain Biodonostia Res Inst, Neurosci Area, San Sebastian, Spain
- [4] Patient-Specific Ipsc-Derived Cardiac Fibroblasts Phenotypes in Lmna CardiomyopathyCIRCULATION, 2021, 144Yang, Jiajia论文数: 0 引用数: 0 h-index: 0Argenziano, Mariana论文数: 0 引用数: 0 h-index: 0Angulo, Mariana Burgos论文数: 0 引用数: 0 h-index: 0McDonald, Thomas V.论文数: 0 引用数: 0 h-index: 0
- [5] Corrected patient-specific, iPSC-derived epithelial sheets for dystrophic epidermolysis bullosaJOURNAL OF INVESTIGATIVE DERMATOLOGY, 2014, 134 : S79 - S79Sebastiano, V.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Pathol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAZhen, H.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAWang, P.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAHaddad, B.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Pathol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USABashkirova, E.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAAmeen, M.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USASiprashvili, Z.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAMelo, S.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USALi, J.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAKim, S.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USALane, A.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAWernig, M.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Pathol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USAOro, A.论文数: 0 引用数: 0 h-index: 0机构: Stanford, Program Epithelial Biol, Stanford, CA USA Stanford, Program Epithelial Biol, Stanford, CA USA
- [6] Modeling mucopolysaccharidosis type VII using patient-specific iPSC-derived neuronsHUMAN GENE THERAPY, 2016, 27 (11) : A78 - A78Bayo-Puxan, N.论文数: 0 引用数: 0 h-index: 0机构: Inst Genet Mol Montpellier, Montpellier, France Univ Barcelona, Inst Biomed, Barcelona, Spain Univ Montpellier, Montpellier, France Inst Genet Mol Montpellier, Montpellier, FranceCreyssels, S.论文数: 0 引用数: 0 h-index: 0机构: Inst Genet Mol Montpellier, Montpellier, France Inst Genet Mol Montpellier, Montpellier, FranceSaliinas, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Montpellier, Montpellier, France UMR 1058 Pathogenesis & Control Chron Infect, Brescia, Italy Inst Genet Mol Montpellier, Montpellier, FrancePescia, C.论文数: 0 引用数: 0 h-index: 0机构: Inst Genet Mol Montpellier, Montpellier, France Univ Montpellier, Montpellier, France Inst Genet Mol Montpellier, Montpellier, FranceBosch, A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Barcelona, Spain Inst Genet Mol Montpellier, Montpellier, FranceVellard, M.论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA USA Inst Genet Mol Montpellier, Montpellier, France论文数: 引用数: h-index:机构:Kremer, E. J.论文数: 0 引用数: 0 h-index: 0机构: Inst Genet Mol Montpellier, Montpellier, France Univ Montpellier, Montpellier, France Inst Genet Mol Montpellier, Montpellier, France
- [7] Lipidomic profiling of patient-specific iPSC-derived hepatocyte-like cellsDISEASE MODELS & MECHANISMS, 2017, 10 (09) : 1141 - 1153Kiamehr, Mostafa论文数: 0 引用数: 0 h-index: 0机构: Univ Tampere, Fac Med & Life Sci, Tampere 33520, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandViiri, Leena E.论文数: 0 引用数: 0 h-index: 0机构: Univ Tampere, Fac Med & Life Sci, Tampere 33520, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandVihervaara, Terhi论文数: 0 引用数: 0 h-index: 0机构: Zora Biosci, Espoo 02150, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandKoistinen, Kaisa M.论文数: 0 引用数: 0 h-index: 0机构: Zora Biosci, Espoo 02150, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandHilvo, Mika论文数: 0 引用数: 0 h-index: 0机构: Zora Biosci, Espoo 02150, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandEkroos, Kim论文数: 0 引用数: 0 h-index: 0机构: Zora Biosci, Espoo 02150, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandKakela, Reijo论文数: 0 引用数: 0 h-index: 0机构: Univ Helsinki, Dept Biosci, FIN-00014 Helsinki, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, FinlandAalto-Setala, Katriina论文数: 0 引用数: 0 h-index: 0机构: Univ Tampere, Fac Med & Life Sci, Tampere 33520, Finland Tampere Univ Hosp, Heart Hosp, Tampere 33520, Finland Univ Tampere, Fac Med & Life Sci, Tampere 33520, Finland
- [8] The effect of PTC124 on choroideremia fibroblasts and iPSC-derived RPE raises considerations for therapySCIENTIFIC REPORTS, 2018, 8Torriano, Simona论文数: 0 引用数: 0 h-index: 0机构: INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France Univ Montpellier, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceErkilic, Nejla论文数: 0 引用数: 0 h-index: 0机构: INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France Univ Montpellier, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceBaux, David论文数: 0 引用数: 0 h-index: 0机构: CHRU Montpellier, Lab Mol Genet, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceCereso, Nicolas论文数: 0 引用数: 0 h-index: 0机构: INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France Univ Montpellier, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceDe Luca, Valerie论文数: 0 引用数: 0 h-index: 0机构: INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France Univ Montpellier, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France论文数: 引用数: h-index:机构:Moosajee, Mariya论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Ophthalmol, London, England INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceRoux, Anne-Francoise论文数: 0 引用数: 0 h-index: 0机构: CHRU Montpellier, Lab Mol Genet, Montpellier, France Univ Montpellier, EA 7402, Lab Rare Genet Dis, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, FranceHamel, Christian P.论文数: 0 引用数: 0 h-index: 0机构: INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France Univ Montpellier, Montpellier, France CHRU Montpellier, Dept Ophthalmol, Montpellier, France CHRU Montpellier, Ctr Reference Genet Sensory Dis, Montpellier, France INSERM, U1051, Inst Neurosci Montpellier, Montpellier, France论文数: 引用数: h-index:机构:
- [9] The effect of PTC124 on choroideremia fibroblasts and iPSC-derived RPE raises considerations for therapyScientific Reports, 8Simona Torriano论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyNejla Erkilic论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyDavid Baux论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyNicolas Cereso论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyValerie De Luca论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyIsabelle Meunier论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyMariya Moosajee论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyAnne-Francoise Roux论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyChristian P. Hamel论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of OphthalmologyVasiliki Kalatzis论文数: 0 引用数: 0 h-index: 0机构: Inserm U1051,Department of Ophthalmology
- [10] Patient-specific iPSC-derived cardiomyocytes reveal variable phenotypic severity of Brugada syndromeEBIOMEDICINE, 2023, 95Sun, Yaxun论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaSu, Jun论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaWang, Xiaochen论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaWang, Jue论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaGuo, Fengfeng论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaQiu, Hangyuan论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaFan, Hangping论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaCai, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaWang, Hao论文数: 0 引用数: 0 h-index: 0机构: Hangzhou Womens Hosp, Prenatal Diag Ctr, Hangzhou 310008, Zhejiang, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaLin, Miao论文数: 0 引用数: 0 h-index: 0机构: Wenzhou Cent Hosp, Dept Cardiol, Wenzhou 325000, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaWang, Wei论文数: 0 引用数: 0 h-index: 0机构: Jiangxi Prov Peoples Hosp, Jiangxi Cardiovasc Dis Res Inst, Nanchang 330006, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaFeng, Ye论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaFu, Guosheng论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaGong, Tingyu论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China Zhejiang Shuren Univ, Shulan Int Med Coll, Hangzhou 310015, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaLiang, Ping论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sch Med, Key Lab Combined Multiorgan Transplantat, Minist Publ Hlth,Affiliated Hosp 1, Hangzhou 310003, Peoples R China Zhejiang Univ, Inst Translat Med, Hangzhou 310029, Peoples R China 268 Kaixuan Rd,North Block Cent Bldg,Room 404, Hangzhou 310029, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R ChinaJiang, Chenyang论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China 3 Qingchun East Rd, Hangzhou 310016, Peoples R China Zhejiang Univ, Sir Run Run Shaw Hosp, Dept Cardiol, Sch Med, Hangzhou 310009, Peoples R China