A Novel AAV8-Based Gene Therapy for Duchenne Muscular Dystrophy: Preclinical Studies in the Mdx Mouse

被引：0
|
作者：
Kim, S. [1 ]
Buss, N. [1 ]
Patel, H. [1 ]
Yang, L. [1 ]
Kim, K. [1 ]
Chan, G. [1 ]
Qiao, C. [1 ]
Liu, Y. [1 ]
Fiscella, M. [1 ]
Danos, O. [1 ]
机构：
[1] REGENXBIO Inc, Washington, DC USA
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P308
引用
收藏
页码：A122 / A123
页数：2
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