A Novel AAV8-Based Gene Therapy for Duchenne Muscular Dystrophy: Preclinical Studies in the Mdx Mouse

被引：0

作者：

Kim, S. ^{[1
]}

Buss, N. ^{[1
]}

Patel, H. ^{[1
]}

Yang, L. ^{[1
]}

Kim, K. ^{[1
]}

Chan, G. ^{[1
]}

Qiao, C. ^{[1
]}

Liu, Y. ^{[1
]}

Fiscella, M. ^{[1
]}

Danos, O. ^{[1
]}

机构：

[1] REGENXBIO Inc, Washington, DC USA

来源：

HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P308

引用

页码：A122 / A123

页数：2

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