Splicing modulation therapy for a variety of ABCA4 mutations underlying Stargardt disease

被引：0
|
作者：
Garanto, A. [1 ,2 ,7 ]
Tomkiewicz, T. Z. [2 ,6 ]
Suarez-Herrera, N. [2 ,6 ]
Khan, M. [2 ,6 ]
Sangermano, R. [2 ,6 ]
Bauwens, M. [3 ,4 ]
Naessens, S. [3 ,4 ]
De Baere, E. [3 ,4 ]
Cheetham, M. E. [5 ]
Cremers, F. P. M. [2 ,6 ]
Collin, R. W. J. [2 ,6 ]
机构：
[1] Radboud Univ Nijmegen, Med Ctr, Dept Pediat, Nijmegen, Netherlands
[2] Radboud Univ Nijmegen, Med Ctr, Dept Human Genet, Nijmegen, Netherlands
[3] Univ Ghent, Ctr Med Genet, Ghent, Belgium
[4] Ghent Univ Hosp, Ghent, Belgium
[5] UCL Inst Ophthalmol, London, England
[6] Radboud Univ Nijmegen, Med Ctr, Donders Inst Brain Cognit & Behav, Nijmegen, Netherlands
[7] Radboud Univ Nijmegen, Med Ctr, Radboud Inst Mol Life Sci, Nijmegen, Netherlands
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P148
引用
收藏
页码：A74 / A74
页数：1
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