Splicing modulation therapy for a variety of ABCA4 mutations underlying Stargardt disease

被引：0

作者：

Garanto, A. ^{[1
,2
,7
]}

Tomkiewicz, T. Z. ^{[2
,6
]}

Suarez-Herrera, N. ^{[2
,6
]}

Khan, M. ^{[2
,6
]}

Sangermano, R. ^{[2
,6
]}

Bauwens, M. ^{[3
,4
]}

Naessens, S. ^{[3
,4
]}

De Baere, E. ^{[3
,4
]}

Cheetham, M. E. ^{[5
]}

Cremers, F. P. M. ^{[2
,6
]}

Collin, R. W. J. ^{[2
,6
]}

机构：

[1] Radboud Univ Nijmegen, Med Ctr, Dept Pediat, Nijmegen, Netherlands

[2] Radboud Univ Nijmegen, Med Ctr, Dept Human Genet, Nijmegen, Netherlands

[3] Univ Ghent, Ctr Med Genet, Ghent, Belgium

[4] Ghent Univ Hosp, Ghent, Belgium

[5] UCL Inst Ophthalmol, London, England

[6] Radboud Univ Nijmegen, Med Ctr, Donders Inst Brain Cognit & Behav, Nijmegen, Netherlands

[7] Radboud Univ Nijmegen, Med Ctr, Radboud Inst Mol Life Sci, Nijmegen, Netherlands

来源：

HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P148

引用

页码：A74 / A74

页数：1

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