Gene transfer into haematopoietic stem cells for the treatment of ADA-deficient SCID

被引：0
|
作者：
Aiuti, A
Benninghoff, U
Cassani, B
Cattaneo, F
Andolfi, G
Mirolo, M
Callegaro, L
Tabucchi, A
Carlucci, F
Eibl, M
Aker, M
Slavin, S
Miniero, R
Roncarolo, M
San Raffaele, CB
机构：
[1] San Raffaele Telethon Inst Gene Therapy, HSR, TIGET, Milan, Italy
[2] Univ Siena, I-53100 Siena, Italy
[3] Immunol Tagesklin, Vienna, Austria
[4] Hadassah Univ Hosp, IL-91120 Jerusalem, Israel
来源：
BONE MARROW TRANSPLANTATION | 2005年 / 35卷
关键词：
D O I：
暂无
中图分类号：
Q6 [生物物理学];
学科分类号：
071011 ;
摘要：
引用
收藏
页码：S17 / S17
页数：1
相关论文
共 50 条
  • [21] ADA-deficient SCID is associated with a specific microenvironment and bone phenotype characterized by RANKL/OPG imbalance and osteoblast insufficiency
    Sauer, Aisha V.
    Mrak, Emanuela
    Hernandez, Raisa Jofra
    Zacchi, Elena
    Cavani, Francesco
    Casiraghi, Miriam
    Grunebaum, Eyal
    Roifman, Chaim M.
    Cervi, Maria C.
    Ambrosi, Alessandro
    Carlucci, Filippo
    Roncarolo, Maria Grazia
    Villa, Anna
    Rubinacci, Alessandro
    Aiuti, Alessandro
    BLOOD, 2009, 114 (15) : 3216 - 3226
  • [22] Clinical Significance of Inherited Chromosomally Integrated HHV-6 (iciHHV-6) in the Setting of ADA-Deficient SCID
    Purswani, Pooja
    Hall, Geoffrey
    Mousallem, Talal
    JOURNAL OF CLINICAL IMMUNOLOGY, 2022, 42 (SUPPL 1) : S37 - S37
  • [23] TRANSFER OF THE ADENOSINE-DEAMINASE (ADA) GENE OF A B-LYMPHOBLASTOID CELL-LINE (LCL) TO AN ADA-DEFICIENT LCL BY A MICROCELL-MEDIATED CHROMOSOME TRANSFER TECHNIQUE
    SAWAMI, H
    ITO, K
    NORIOKA, M
    MONDEN, S
    FUJITA, M
    UCHINO, H
    ACTA HAEMATOLOGICA JAPONICA, 1989, 52 (06): : 1033 - 1044
  • [24] Hematopoictic stem cell gene therapy for ADA-SCID
    Aiuti, Alessandro
    Bordignon, Claudio
    Roncarolo, Maria Grazia
    BLOOD CELLS MOLECULES AND DISEASES, 2008, 40 (02) : 250 - 250
  • [25] Clinical implications of inherited chromosomally integrated HHV-6 in the setting of ADA-deficient severe combined immunodeficiency (SCID)
    Purswani, Pooja
    Hall, Geoffrey
    Moorthy, Ganga
    Mousallem, Talal
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY-IN PRACTICE, 2023, 11 (11): : 3553 - +
  • [26] Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC
    Cuvelier, Geoffrey D. E.
    Logan, Brent R.
    Prockop, Susan E.
    Buckley, Rebecca H.
    Kuo, Caroline Y.
    Griffith, Linda M.
    Liu, Xuerong
    Yip, Alison
    Hershfield, Michael S.
    Ayoub, Paul G.
    Moore, Theodore B.
    Dorsey, Morna J.
    O'Reilly, Richard J.
    Kapoor, Neena
    Pai, Sung-Yun
    Kapadia, Malika
    Ebens, Christen L.
    Satter, Lisa R. Forbes
    Burroughs, Lauri M.
    Petrovic, Aleksandra
    Chellapandian, Deepak
    Heimall, Jennifer
    Shyr, David C.
    Rayes, Ahmad
    Bednarski, Jeffrey J.
    Chandra, Sharat
    Chandrakasan, Shanmuganathan
    Gillio, Alfred P.
    Madden, Lisa
    Quigg, Troy C.
    Caywood, Emi H.
    Saldana, Blachy J. Davila
    DeSantes, Kenneth
    Eissa, Hesham
    Goldman, Frederick D.
    Rozmus, Jacob
    Shah, Ami J.
    Vander Lugt, Mark T.
    Thakar, Monica S.
    Parrott, Roberta E.
    Martinez, Caridad
    Leiding, Jennifer W.
    Torgerson, Troy R.
    Pulsipher, Michael A.
    Notarangelo, Luigi D.
    Cowan, Morton J.
    Dvorak, Christopher C.
    Haddad, Elie
    Puck, Jennifer M.
    Kohn, Donald B.
    BLOOD, 2022, 140 (07) : 685 - 705
  • [27] Lentiviral-mediated gene transfer into haematopoietic stem cells
    Woods, NB
    Mikkola, H
    Nilsson, E
    Olsson, K
    Trono, D
    Karlsson, S
    JOURNAL OF INTERNAL MEDICINE, 2001, 249 (04) : 339 - 343
  • [28] Advances in gene transfer into haematopoietic stem cells by adenoviral vectors
    Marini, FC
    Shayakhmetov, D
    Gharwan, H
    Lieber, A
    Andreeff, M
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2002, 2 (08) : 847 - 856
  • [29] Carrier frequency of a nonsense mutation in the adenosine deaminase (ADA) gene implies a high incidence of ADA-deficient severe combined immunodeficiency (SCID) in Somalia and a single, common haplotype indicates common ancestry
    Sanchez, Juan J.
    Monaghan, Gemma
    Borsting, Claus
    Norbury, Gail
    Morling, Niels
    Gaspar, H. Bobby
    ANNALS OF HUMAN GENETICS, 2007, 71 : 336 - 347
  • [30] Effects of Vector Backbone and Pseudotype on Lentiviral Vector-mediated Gene Transfer: Studies in Infant ADA-Deficient Mice and Rhesus Monkeys
    Sarracino, Denise Carbonaro
    Taranta, Alice F.
    Lee, C. Chang I.
    Martinez, Michele
    Lin, Xiangyang
    Wang, Xiaoyan
    Hardee, Cinnamon L.
    Geiger, Sabine
    Kahl, Christoph A.
    Kohn, Donald B.
    MOLECULAR THERAPY, 2014, 22 (10) : 1803 - 1816
12345