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- [12] Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonatesNATURE MEDICINE, 2003, 9 (04) : 463 - 468Schmidt, M论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USACarbonaro, DA论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USASpeckmann, C论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USAWissler, M论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USABohnsack, J论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USAElder, M论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USAAronow, BJ论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USANolta, JA论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USAKohn, DB论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USA Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USAvon Kalle, C论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol & Bone Marrow Transplantat, Los Angeles, CA 90027 USA
- [13] Gene delivery using AAV8 in vivo for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCIDMOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2021, 20 : 765 - 778Carbonaro-Sarracino, Denise A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAChun, Krista论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAClark, Danielle N.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAKaufman, Michael L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAJin, Xiangyang论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAWang, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Gen Internal Med & Hlth Serv Res, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Pediat, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Eli & Edythe Broad Ctr Stem Cells & Regenerat Med, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, 610 Charles E Young Dr E, Los Angeles, CA 90095 USA
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- [15] Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case reportBLOOD, 2007, 109 (02) : 503 - 506Engel, Barbara C.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAPodsakoff, Greg M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAIreland, Joanna L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USASmogorzewska, E. Monika论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USACarbonaro, Denise A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAWilson, Kathy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAShah, Ami论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAKapoor, Neena论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USASweeney, Mirna论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USABorchert, Mark论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USACrooks, Gay M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAWeinberg, Kenneth I.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAParkman, Robertson论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USARosenblatt, Howard M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAWu, Shi-Qi论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAHershfield, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USACandotti, Fabio论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USA
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