Gene transfer into haematopoietic stem cells for the treatment of ADA-deficient SCID

被引：0
|
作者：
Aiuti, A
Benninghoff, U
Cassani, B
Cattaneo, F
Andolfi, G
Mirolo, M
Callegaro, L
Tabucchi, A
Carlucci, F
Eibl, M
Aker, M
Slavin, S
Miniero, R
Roncarolo, M
San Raffaele, CB
机构：
[1] San Raffaele Telethon Inst Gene Therapy, HSR, TIGET, Milan, Italy
[2] Univ Siena, I-53100 Siena, Italy
[3] Immunol Tagesklin, Vienna, Austria
[4] Hadassah Univ Hosp, IL-91120 Jerusalem, Israel
来源：
BONE MARROW TRANSPLANTATION | 2005年 / 35卷
关键词：
D O I：
暂无
中图分类号：
Q6 [生物物理学];
学科分类号：
071011 ;
摘要：
引用
收藏
页码：S17 / S17
页数：1
相关论文
共 50 条
  • [1] Lentiviral vector mediated ADA gene transfer in ADA-deficient SCID mice
    Carbonaro, DA
    Jin, XY
    Senadherra, D
    Pepper, K
    Petersen, D
    Yu, XJ
    Skelton, D
    Kohn, DB
    MOLECULAR THERAPY, 2004, 9 : S68 - S68
  • [2] Advances in gene therapy for ADA-deficient SCID
    Aiuti, A
    CURRENT OPINION IN MOLECULAR THERAPEUTICS, 2002, 4 (05) : 515 - 522
  • [3] TRANSFER OF THE ADA GENE INTO BONE-MARROW CELLS AND PERIPHERAL-BLOOD LYMPHOCYTES FOR THE TREATMENT OF PATIENTS AFFECTED BY ADA-DEFICIENT SCID
    BORDIGNON, C
    HUMAN GENE THERAPY, 1993, 4 (04) : 513 - 520
  • [4] Integration analyses in ADA-deficient SCID patients successfully treated with stem cell gene therapy
    Aiuti, A
    Cassani, B
    Cattaneo, F
    Andolfi, G
    Mirolo, M
    Recchia, A
    Callegaro, L
    Tabucchi, A
    Carlucci, F
    Slavin, S
    Miniero, R
    Mavilio, F
    Roncarolo, MG
    Bordignon, C
    MOLECULAR THERAPY, 2004, 9 : S384 - S385
  • [5] Clinical trials of retroviral-mediated gene transfer to hematopoietic stem cells for ADA-deficient SCID and pediatric HIV-1 infection.
    Kohn, DB
    Candotti, F
    Podsakoff, G
    Engel, B
    Carbonaro, D
    Choi, C
    Cho, G
    Smogorsweska, M
    Church, J
    Shuman, S
    Muul, L
    BLOOD CELLS MOLECULES AND DISEASES, 2002, 28 (03) : 333 - 334
  • [6] ADA-DEFICIENT SCID DIAGNOSED AT 3 YEARS OF AGE
    Preece, Kahn
    Bhatia, Rani
    Wong, Melanie
    INTERNAL MEDICINE JOURNAL, 2012, 42 : 19 - 19
  • [7] MANAGEMENT OF ADA-DEFICIENT SCID PATIENT DURING PREGNANCY
    Shams, Marissa
    JOURNAL OF CLINICAL IMMUNOLOGY, 2016, 36 (03) : 242 - 242
  • [8] Management of ADA-Deficient SCID Patient on Adagen During Pregnancy
    Shams, Marissa
    Kobrynski, Lisa
    JOURNAL OF CLINICAL IMMUNOLOGY, 2019, 39 (08) : 846 - 848
  • [9] Management of ADA-Deficient SCID Patient on Adagen During Pregnancy
    Marissa Shams
    Lisa Kobrynski
    Journal of Clinical Immunology, 2019, 39 : 846 - 848
  • [10] GENE-THERAPY FOR NEONATES WITH ADA-DEFICIENT SCID BY RETROVIRAL-MEDIATED TRANSFER OF THE HUMAN ADA CDNA INTO UMBILICAL-CORD CD34+ CELLS
    KOHN, DB
    WEINBERG, KI
    PARKMAN, R
    LENARSKY, C
    CROOKS, GM
    SHAW, K
    HANLEY, ME
    LAWRENCE, K
    ANNETT, G
    BROOKS, JS
    WARA, D
    ELDER, M
    BOWEN, T
    HERSHFIELD, MS
    BERENSON, RI
    MOEN, RC
    MULLEN, CA
    BLAESE, RM
    JOURNAL OF CELLULAR BIOCHEMISTRY, 1994, : 238 - 238
12345