Systematic evaluation of 2′-Fluoro modified chimeric antisense oligonucleotide-mediated exon skipping in vitro (vol 9, 6078, 2019)

被引：0
|
作者：
Chen, Suxiang [1 ,2 ]
Le, Bao T. [1 ,2 ]
Chakravarthy, Madhuri [1 ,2 ]
Kosbar, Tamer R. [1 ]
Veedu, Rakesh N. [1 ,2 ]
机构：
[1] Murdoch Univ, Ctr Mol Med & Innovat Therapeut, Murdoch, WA 6150, Australia
[2] Perron Inst Neurol & Translat Sci, Perth, WA 6150, Australia
来源：
SCIENTIFIC REPORTS | 2020年 / 10卷 / 01期
关键词：
D O I：
10.1038/s41598-020-63706-0
中图分类号：
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号：
07 ; 0710 ; 09 ;
摘要：
An amendment to this paper has been published and can be accessed via a link at the top of the paper.
引用
收藏
页数：1
相关论文
共 34 条
  • [31] Treatment of DMD 5′ Mutations Through Two Different exon2 Skipping Strategies: Intramuscular Delivery of rAAV9. snRNA Mediated Skipping and Antisense Morpholino Oligomers
    Simmons, Tabatha R.
    Wein, Nicolas
    Vulin-Chaffiol, Adeline
    Heller, Kristin
    Rutherford, Andrea
    Rodino-Klapac, Louise
    Flanigan, Kevin M.
    MOLECULAR THERAPY, 2015, 23 : S202 - S202
  • [32] Rational Design of Short Locked Nucleic Acid-Modified 2′-O-Methyl Antisense Oligonucleotides for Efficient Exon-Skipping In Vitro
    Le, Bao T.
    Adams, Abbie M.
    Fletcher, Susan
    Wilton, Stephen D.
    Veedu, Rakesh N.
    MOLECULAR THERAPY-NUCLEIC ACIDS, 2017, 9 : 155 - 161
  • [33] Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B (vol 16, e1008690, 2020)
    Krooss, Simon
    Werwitzke, Sonja
    Kopp, Johannes
    Rovai, Alice
    Varnholt, Dirk
    Wachs, Amelie S.
    Goyenvalle, Aurelie
    Aartsma-Rus, Annemieke
    Ott, Michael
    Tiede, Andreas
    Langemeier, Jorg
    Bohne, Jens
    PLOS GENETICS, 2021, 17 (01):
  • [34] Evaluation of anhydrohexitol nucleic acid, cyclohexenyl nucleic acid and D-altritol nucleic acid-modified 2′-O-methyl RNA mixmer antisense oligonucleotides for exon skipping in vitro
    Le, Bao T.
    Chen, Suxiang
    Abramov, Mikhail
    Herdewijn, Piet
    Veedu, Rakesh N.
    CHEMICAL COMMUNICATIONS, 2016, 52 (92) : 13467 - 13470
1234