共 34 条
- [21] Evaluation of 2′-Deoxy-2′-fluoro Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular Dystrophy MOLECULAR THERAPY-NUCLEIC ACIDS, 2015, 4 : e265
- [24] Inhibition of IL-1 Signaling by Antisense Oligonucleotide-mediated Exon Skipping of IL-1 Receptor Accessory Protein (IL-1RAcP) MOLECULAR THERAPY-NUCLEIC ACIDS, 2013, 2 : e66
- [28] Nucleobase-modified antisense oligonucleotides containing 5-(phenyltriazol)-2′-deoxyuridine nucleotides induce exon-skipping in vitro RSC ADVANCES, 2017, 7 (86): : 54542 - 54545
- [30] A novel human muscle cell model of Duchenne muscular dystrophy created by CRISPR/Cas9 and evaluation of antisense-mediated exon skipping Journal of Human Genetics, 2018, 63 : 365 - 375