Early-onset reduced bone mineral density in patients with pyruvate kinase deficiency

被引:4
|
作者
Al-Samkari, Hanny [1 ]
Grace, Rachael F. [2 ]
Glenthoj, Andreas [3 ]
Andres, Oliver [4 ]
Barcellini, Wilma [5 ]
Galacteros, Frederic [6 ]
Kuo, Kevin H. M. [7 ]
Layton, D. Mark [8 ]
Morado Arias, Marta [9 ]
Viprakasit, Vip [10 ]
Dong, Yan [11 ]
Tai, Feng [11 ]
Hawkins, Peter [11 ]
Gheuens, Sarah [11 ]
Morales-Arias, Jaime [11 ]
Gilroy, Keely S. [11 ]
Porter, John B. [12 ]
van Beers, Eduard J. [13 ]
机构
[1] Harvard Med Sch, Massachusetts Gen Hosp, Div Hematol, Zero Emerson Pl,Suite 118,Off 112, Boston, MA 02114 USA
[2] Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA
[3] Copenhagen Univ Hosp, Dept Haematol, Rigshosp, Copenhagen, Denmark
[4] Univ Wurzburg, Dept Paediat, Wurzburg, Germany
[5] Fdn IRCCS Ca Granda Osped Maggiore Policlin, Milan, Italy
[6] CHU Henri Mondor, Unite Malad Genet Globule Rouge, Creteil, France
[7] Univ Toronto, Div Hematol, Toronto, ON, Canada
[8] Imperial Coll Healthcare NHS Trust, Hammersmith Hosp, London, England
[9] Hosp Univ La Paz, Hematol Dept, Madrid, Spain
[10] Mahidol Univ, Siriraj Hosp, Fac Med, Siriraj Thalassemia Ctr, Bangkok, Thailand
[11] Agios Pharmaceut Inc, Cambridge, MA USA
[12] Univ Coll London Hosp, Haematol Dept, London, England
[13] Univ Utrecht, Univ Med Ctr Utrecht, Van Creveldklin, Benign Hematol Ctr, Utrecht, Netherlands
关键词
THALASSEMIA; MITAPIVAT;
D O I
10.1002/ajh.26830
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:E57 / E60
页数:4
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