[1] Harvard Med Sch, Massachusetts Gen Hosp, Div Hematol, Zero Emerson Pl,Suite 118,Off 112, Boston, MA 02114 USA
[2] Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA
[3] Copenhagen Univ Hosp, Dept Haematol, Rigshosp, Copenhagen, Denmark
[4] Univ Wurzburg, Dept Paediat, Wurzburg, Germany
[5] Fdn IRCCS Ca Granda Osped Maggiore Policlin, Milan, Italy
[6] CHU Henri Mondor, Unite Malad Genet Globule Rouge, Creteil, France
[7] Univ Toronto, Div Hematol, Toronto, ON, Canada
[8] Imperial Coll Healthcare NHS Trust, Hammersmith Hosp, London, England
[9] Hosp Univ La Paz, Hematol Dept, Madrid, Spain
[10] Mahidol Univ, Siriraj Hosp, Fac Med, Siriraj Thalassemia Ctr, Bangkok, Thailand
[11] Agios Pharmaceut Inc, Cambridge, MA USA
[12] Univ Coll London Hosp, Haematol Dept, London, England
[13] Univ Utrecht, Univ Med Ctr Utrecht, Van Creveldklin, Benign Hematol Ctr, Utrecht, Netherlands