共 50 条
- [31] Impact Of Nusinersen Treatment On Measures Of Exercise Intolerance In Spinal Muscular AtrophyMEDICINE & SCIENCE IN SPORTS & EXERCISE, 2023, 55 (09) : 964 - 964Uher, David论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Irving Med Ctr, New York, NY USA Columbia Univ, Irving Med Ctr, New York, NY USAGoodwin, Ashley M.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Irving Med Ctr, New York, NY USA Columbia Univ, Irving Med Ctr, New York, NY USADe Vivo, Darryl C.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Irving Med Ctr, New York, NY USA Columbia Univ, Irving Med Ctr, New York, NY USAMontes, Jacqueline论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Irving Med Ctr, New York, NY USA Columbia Univ, Irving Med Ctr, New York, NY USA论文数: 引用数: h-index:机构:
- [32] Nusinersen Treatment for Spinal Muscular Atrophy: Retrospective Multicenter Study of Pediatric and Adult Patients in KuwaitNEUROLOGY INTERNATIONAL, 2024, 16 (03): : 631 - 642AlTawari, Asma论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitZakaria, Mohammad论文数: 0 引用数: 0 h-index: 0机构: Al Adan Hosp, Dept Pediat, Hadiya 47000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitKamel, Walaa论文数: 0 引用数: 0 h-index: 0机构: Ibn Sina Hosp, Neurol Dept, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitShaalan, Nayera论文数: 0 引用数: 0 h-index: 0机构: Ibn Sina Hosp, Neurol Dept, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitElghazawi, Gamal Ahmed Ismail论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAli, Mohamed Esmat Anwar论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitSalota, Dalia论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAttia, Amr论文数: 0 引用数: 0 h-index: 0机构: Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitElanay, Ehab Elsayed Ali论文数: 0 引用数: 0 h-index: 0机构: Al Adan Hosp, Dept Pediat, Hadiya 47000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitShalaby, Osama论文数: 0 引用数: 0 h-index: 0机构: Al Jahra Hosp, Dept Pediat, Al Jahra 003200, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitAlqallaf, Fatema论文数: 0 引用数: 0 h-index: 0机构: Mubarak Hosp, Pediat Dept, Neurol Unit, Jabriya 46300, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitMitic, Vesna论文数: 0 引用数: 0 h-index: 0机构: Al Farwaniya Hosp, Pediat Dept, Al Farwaniya 85000, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, KuwaitBastaki, Laila论文数: 0 引用数: 0 h-index: 0机构: Kuwait Med Genet Ctr, Shuwaikh Industrial 70050, Kuwait Al Sabah Hosp, Pediat Dept, Neurol Unit, Kuwait 70050, Kuwait
- [33] Intrathecal nusinersen administration in adult spinal muscular atrophy patients with complex spinal anatomyTHERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2020, 13Cordts, Isabell论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyLingor, Paul论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyFriedrich, Benjamin论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyPernpeintner, Verena论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyZimmer, Claus论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyDeschauer, Marcus论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, GermanyMaegerlein, Christian论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Munich, Klinikum Rechts Isar, Dept Diagnost & Intervent Neuroradiol, Munich, Germany Tech Univ Munich, Klinikum Rechts Isar, Dept Neurol, Ismaninger Str 22, D-81675 Munich, Germany
- [34] Respiratory outcome of spinal muscular atrophy type 1 patients treated with nusinersenPEDIATRICS INTERNATIONAL, 2022, 64 (01)Ergenekon, Almala Pinar论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyYegit, Cansu Yilmaz论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyCenk, Muruvvet论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyGokdemir, Yasemin论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyEralp, Ela Erdem论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyOzturk, Gulten论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Neurol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyUnver, Olcay论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Neurol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyCoskun, Ozge Kenis论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Dept Phys Med & Rehabil, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeySaygi, Evrim Karadag论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Dept Phys Med & Rehabil, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyTurkdogan, Dilsad论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Neurol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, TurkeyKaradag, Bulent论文数: 0 引用数: 0 h-index: 0机构: Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey Marmara Univ, Sch Med, Div Pediat Pulmonol, Istanbul, Turkey
- [35] Respiratory Needs in Patients with Type 1 Spinal Muscular Atrophy Treated with NusinersenJOURNAL OF PEDIATRICS, 2020, 219 : 223 - +Sansone, Valeria A.论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy Univ Milan, Neurorehabil Unit, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyPirola, Alice论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyAlbamonte, Emilio论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyPane, Marika论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Rome, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyLizio, Andrea论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyD'Amico, Adele论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Unit Neuromuscular & Neurodegenerat Disorders, Dept Neurosci, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyCatteruccia, Michela论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Unit Neuromuscular & Neurodegenerat Disorders, Dept Neurosci, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyCutrera, Renato论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Dept Pediat, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyBruno, Claudio论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Ctr Translat & Expt Myol, Genoa, Italy NEMO Clin Ctr Milan, Milan, ItalyPedemonte, Marina论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Ctr Translat & Expt Myol, Genoa, Italy NEMO Clin Ctr Milan, Milan, ItalyMessina, Sonia论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Messina NEMO Sud, Messina, Italy Univ Policlin Messina, Dept Neurosci, Messina, Italy NEMO Clin Ctr Milan, Milan, ItalyRao, Fabrizio论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyRoma, Elisabetta论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalySalmin, Francesca论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyCoratti, Giorgia论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Gemelli, Dept Child Neurol, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyDi Bari, Alessandra论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Milan, Milan, Italy NEMO Clin Ctr Milan, Milan, ItalyDe Sanctis, Roberto论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Rome, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyPera, Carmela Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Gemelli, Dept Child Neurol, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalySframeli, Maria论文数: 0 引用数: 0 h-index: 0机构: NEMO Clin Ctr Messina NEMO Sud, Messina, Italy NEMO Clin Ctr Milan, Milan, ItalyPiastra, Marco论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Gemelli, Dept Child Neurol, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyMacagno, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Gemelli, Dept Child Neurol, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyVita, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Messina, Dept Neurosci, Messina, Italy NEMO Clin Ctr Milan, Milan, ItalyBertini, Enrico论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Unit Neuromuscular & Neurodegenerat Disorders, Dept Neurosci, Rome, Italy NEMO Clin Ctr Milan, Milan, ItalyMercuri, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Univ Policlin Gemelli, Dept Child Neurol, Rome, Italy NEMO Clin Ctr Milan, Milan, Italy
- [36] Respiratory management of spinal muscular atrophy type 1 patients treated with NusinersenPEDIATRIC PULMONOLOGY, 2022, 57 (06) : 1505 - 1512Menard, Joris论文数: 0 引用数: 0 h-index: 0机构: Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceSeferian, Andreea M.论文数: 0 引用数: 0 h-index: 0机构: Hop Armand Trousseau, I Mot, Paris, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceFleurence, Emmanuelle论文数: 0 引用数: 0 h-index: 0机构: Hlth Ctr Children & Adolescents, ESEAN APF, Nantes, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceBarzic, Audrey论文数: 0 引用数: 0 h-index: 0机构: Fdn Ildys, Dept Pediat, Brest, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceBinoche, Alexandra论文数: 0 引用数: 0 h-index: 0机构: CHU Lille, Pediat Intens Care Unit Dept, Lille, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceLabouret, Geraldine论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Dept Pediat Pulmonol & Allergol, Toulouse, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceCoutier, Laurianne论文数: 0 引用数: 0 h-index: 0机构: Hop Mere Enfant, Reference Ctr Cyst Fibrosis, Dept Pediat Pulmonol & Allergol, Bron, France Lyon 1 Univ, CNRL, U1028, Lyon, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceVuillerot, Carole论文数: 0 引用数: 0 h-index: 0机构: Hosp Civils Lyon, Hop Mere Enfant, Serv Reeduc Pediat Infantile LEscale, Lyon, France Lyon Univ, CNRS, INSERM, Neuromyogen Inst,UMR 5310,U1219, Lyon, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceBieleu, Blaise M.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Hop Raymond Poincare, AP HP, Dept Pediat Neurol, Garches, France Univ Paris Saclay, Hop Raymond Poincare, AP HP, ICU, Garches, France Ctr Reference Malad Neuromusculaires Garches Neck, Ctr Nord Est Ile de France, Reseau Natl Malad Neuromusculaires, FILNEMUS, Garches, France European Reference Ctr Network Euro NMD ERN, Paris, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, Francede la Banda, Marta Gomez Garcia论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Hop Raymond Poincare, AP HP, Dept Pediat Neurol, Garches, France Univ Paris Saclay, Hop Raymond Poincare, AP HP, ICU, Garches, France Ctr Reference Malad Neuromusculaires Garches Neck, Ctr Nord Est Ile de France, Reseau Natl Malad Neuromusculaires, FILNEMUS, Garches, France European Reference Ctr Network Euro NMD ERN, Paris, France Hop Raymond Poincare, AP HP, Paris 5, Inst Myol,URC APHP Paris Saclay 4, Garche, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceCorvol, Harriet论文数: 0 引用数: 0 h-index: 0机构: Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, France Sorbonne Univ, Ctr Rech St Antoine CRSA, Paris, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceServais, Laurent论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England Ctr Hosp Univ Liege, Univ Hosp Liege, Dept Pediat, Div Child Neurol,Reference Ctr Neuromuscular Dis, Liege, Belgium Univ Liege, Liege, Belgium Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, FranceTaytard, Jessica论文数: 0 引用数: 0 h-index: 0机构: Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, France Sorbonne Univ, INSERM, UMRS1158 Neurophysiol Resp Expt & Clin, Paris, France European Reference Network Lung ERN Lung, Paris, France Armand Trousseau Univ Hosp, Dept Pediat Pulmonol, Paris, France
- [37] Objective and Subjective impact of Nusinersen in Spinal Muscular AtrophyEUROPEAN JOURNAL OF NEUROLOGY, 2020, 27 : 872 - 872Rodriguez Alvarez-Cienfuegos, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, SpainMonton Alvarez, F. I.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, SpainGutierrez Martinez, A.论文数: 0 引用数: 0 h-index: 0机构: Complejo Hosp Univ Insular Maternoinfantil, Neurol, Las Palmas Gran Canaria, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, SpainFregel Rodriguez, C.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, SpainDiez, J. Aleman论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, SpainClaverie, I. Hernandez-Rojo论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Severo Ochoa, Udm Afyc Madrid Sur, Madrid, Spain Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain
- [38] Treatment with nusinersen in adult patients with spinal muscle atrophy in SloveniaEUROPEAN JOURNAL OF NEUROLOGY, 2020, 27 : 868 - 868Leonardis, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaPuksic, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaAvbelj, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaPetek, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaLuksa, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaVucina, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaKranjc, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaKlinar, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, SloveniaKoritnik, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Ljubljana, Ljubljana, Slovenia Univ Med Ctr Ljubljana, Ljubljana, Slovenia
- [39] Respiratory assessment in a spinal muscular atrophy infant treated with nusinersenPEDIATRICS INTERNATIONAL, 2019, 61 (10) : 1051 - 1053Ogawa, Kazuya论文数: 0 引用数: 0 h-index: 0机构: Oita Univ, Fac Med, Dept Pediat, 1-1 Idaigaoka, Yufu, Oita 8795593, Japan Oita Univ, Fac Med, Dept Pediat, 1-1 Idaigaoka, Yufu, Oita 8795593, Japan论文数: 引用数: h-index:机构:Kobayashi, Osamu论文数: 0 引用数: 0 h-index: 0机构: Oita Univ, Fac Med, Dept Pediat, 1-1 Idaigaoka, Yufu, Oita 8795593, Japan Oita Univ, Fac Med, Dept Pediat, 1-1 Idaigaoka, Yufu, Oita 8795593, JapanNakashima, Misaki论文数: 0 引用数: 0 h-index: 0机构: Nakatsu Municipal Hosp, Pediat, Yufu, Oita, Japan Oita Univ, Fac Med, Dept Pediat, 1-1 Idaigaoka, Yufu, Oita 8795593, Japan论文数: 引用数: h-index:机构:
- [40] Neurodegeneration Biomarkers in Adult Spinal Muscular Atrophy (SMA) Patients Treated with NusinersenINTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2024, 25 (07)Andres-Benito, Pol论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, Spain Inst Hlth Carlos III, Network Ctr Biomed Res Neurodegenerat Dis, CIBERNED, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainVazquez-Costa, Juan Francisco论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ & PolitecnLa Fe & IIS La Fe, Ctr Invest Biomed Red Enfermedades Raras CIBERER, Dept Neurol, Neuromuscular Unit, Valencia 46026, Spain Hosp Univ & Politecn La Fe & IIS La Fe, Ctr Invest Biomed Red Enfermedades Raras CIBERER, Dept Neurol, ERN NMD Grp, Valencia 46026, Spain Univ Valencia, Dept Med, Valencia 46021, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainGarzon, Nancy Carolina Nungo论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ & Politecn La Fe & IIS La Fe, Ctr Invest Biomed Red Enfermedades Raras CIBERER, Dept Neurol, ERN NMD Grp, Valencia 46026, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainColomina, Maria J.论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Univ Hosp, Univ Barcelona, Anesthesia & Crit Care Dept, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainMarco, Carla论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Univ Hosp, Dept Neurol, Funct Unit Amyotroph Lateral Sclerosis UFELA, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainGonzalez, Laura论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Univ Hosp, Dept Neurol, Funct Unit Amyotroph Lateral Sclerosis UFELA, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainTerrafeta, Cristina论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Univ Hosp, Dept Neurol, Funct Unit Amyotroph Lateral Sclerosis UFELA, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, SpainDominguez, Raul论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, Spain Inst Hlth Carlos III, Network Ctr Biomed Res Neurodegenerat Dis, CIBERNED, Barcelona 08907, Spain Bellvitge Univ Hosp, Dept Neurol, Funct Unit Amyotroph Lateral Sclerosis UFELA, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, Spain论文数: 引用数: h-index:机构:Povedano, Monica论文数: 0 引用数: 0 h-index: 0机构: Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, Spain Inst Hlth Carlos III, Network Ctr Biomed Res Neurodegenerat Dis, CIBERNED, Barcelona 08907, Spain Bellvitge Univ Hosp, Dept Neurol, Funct Unit Amyotroph Lateral Sclerosis UFELA, Barcelona 08907, Spain Bellvitge Inst Biomed Res IDIBELL, Neurol Dis & Neurogenet Grp, Barcelona 08907, Spain