The impact of nusinersen on respiratory function in adult patients with spinal muscular atrophy after 1.5 years of treatment

被引：0
|
作者：
Simek, Pija Puksic [1 ]
Tratnjek, Manca Groznik [1 ]
Koritnik, Blaz [1 ]
Leonardis, Lea [1 ]
机构：
[1] UKC Ljubljana, Ljubljana, Slovenia
来源：
EUROPEAN RESPIRATORY JOURNAL | 2024年 / 64卷
关键词：
D O I：
10.1183/13993003.congress-2024.PA1442
中图分类号：
R56 [呼吸系及胸部疾病];
学科分类号：
摘要：
引用
收藏
页数：2
相关论文
共 50 条
  • [21] Nusinersen treatment in adult patients with spinal muscular atrophy: a safety analysis of laboratory parameters
    Benjamin Stolte
    Michael Nonnemacher
    Kathrin Kizina
    Saskia Bolz
    Andreas Totzeck
    Andreas Thimm
    Bernd Wagner
    Cornelius Deuschl
    Christoph Kleinschnitz
    Tim Hagenacker
    Journal of Neurology, 2021, 268 : 4667 - 4679
  • [22] Nusinersen treatment of adult patients with spinal muscular atrophy: Clinical experience from Slovenia
    Stublar, A.
    Petek, K.
    Luksa, M.
    Kranjc, P.
    Baruca, M.
    Avbelj, P.
    Leonardis, L.
    Puksi, P.
    Koritnik, B.
    Zunkovi, B.
    Ojstersek, M. Vuina
    Subic, A.
    Snoj, Z.
    Salapura, V.
    EUROPEAN JOURNAL OF NEUROLOGY, 2021, 28 : 832 - 832
  • [23] Nusinersen treatment in adult patients with spinal muscular atrophy: a safety analysis of laboratory parameters
    Stolte, Benjamin
    Nonnemacher, Michael
    Kizina, Kathrin
    Bolz, Saskia
    Totzeck, Andreas
    Thimm, Andreas
    Wagner, Bernd
    Deuschl, Cornelius
    Kleinschnitz, Christoph
    Hagenacker, Tim
    JOURNAL OF NEUROLOGY, 2021, 268 (12) : 4667 - 4679
  • [24] An early Transcriptomic Investigation in Adult Patients with Spinal Muscular Atrophy Under Treatment with Nusinersen
    Liguori, Maria
    Bianco, Annalisa
    Introna, Alessandro
    Consiglio, Arianna
    Milella, Giammarco
    Abbatangelo, Elena
    D'Errico, Eustachio
    Licciulli, Flavio
    Grillo, Giorgio
    Simone, Isabella Laura
    JOURNAL OF MOLECULAR NEUROSCIENCE, 2024, 74 (04)
  • [25] Nusinersen experience in adult patients with Spinal muscular atrophy in Greece.
    Xirou, S.
    Melemeni, A.
    Tsaroucha, A.
    Chatziioannou, A.
    Krokidis, M.
    Stolis, O.
    Fardellas, K.
    Kararizou, E.
    Papadopoulos, C.
    Papadimas, G.
    EUROPEAN JOURNAL OF NEUROLOGY, 2021, 28 : 395 - 395
  • [26] Spinal Muscular Atrophy - expert recommendations for the use of nusinersen in adult patients
    Hagenacker, Tim
    Hermann, Andreas
    Kamm, Christoph
    Walter, Maggie C.
    Weiler, Markus
    Guenther, Rene
    Wurster, Claudia D.
    Kleinschnitz, Christoph
    FORTSCHRITTE DER NEUROLOGIE PSYCHIATRIE, 2019, 87 (12) : 703 - 710
  • [27] Effect of Nusinersen on Respiratory and Bulbar Function in Children with Spinal Muscular Atrophy: Correspondence
    Daungsupawong, Hinpetch
    Wiwanitkit, Viroj
    NEUROPEDIATRICS, 2025, 56 (01) : 61 - 62
  • [28] Nusinersen in pediatric and adult patients with type III spinal muscular atrophy
    Pera, Maria Carmela
    Coratti, Giorgia
    Bovis, Francesca
    Pane, Marika
    Pasternak, Amy
    Montes, Jacqueline
    Sansone, Valeria A.
    Dunaway Young, Sally
    Duong, Tina
    Messina, Sonia
    Mizzoni, Irene
    D'Amico, Adele
    Civitello, Matthew
    Glanzman, Allan M.
    Bruno, Claudio
    Salmin, Francesca
    Morando, Simone
    De Sanctis, Roberto
    Sframeli, Maria
    Antonaci, Laura
    Frongia, Anna Lia
    Rohwer, Annemarie
    Scoto, Mariacristina
    De Vivo, Darryl C.
    Darras, Basil T.
    Day, John
    Martens, William
    Patanella, Katia A.
    Bertini, Enrico
    Muntoni, Francesco
    Finkel, Richard
    Mercuri, Eugenio
    ANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY, 2021, 8 (08): : 1622 - 1634
  • [29] Nusinersen Treatment in Adults With Spinal Muscular Atrophy
    Duong, Tina
    Wolford, Connie
    McDermott, Michael P.
    Macpherson, Chelsea E.
    Pasternak, Amy
    Glanzman, Allan M.
    Martens, William B.
    Kichula, Elizabeth
    Darras, Basil T.
    De Vivo, Darryl C.
    Zolkipli-Cunningham, Zarazuela
    Finkel, Richard S.
    Zeineh, Michael
    Wintermark, Max
    Sampson, Jacinda
    Hagerman, Katharine A.
    Young, Sally Dunaway
    Day, John W.
    NEUROLOGY-CLINICAL PRACTICE, 2021, 11 (03) : E317 - E327
  • [30] Clinical and Electrophysiological Changes in Pediatric Spinal Muscular Atrophy after 2 Years of Nusinersen Treatment
    Axente, Mihaela
    Mirea, Andrada
    Sporea, Corina
    Padure, Liliana
    Dragoi, Cristina Manuela
    Nicolae, Alina Crenguta
    Ion, Daniela Adriana
    PHARMACEUTICS, 2022, 14 (10)
12345