The impact of nusinersen on respiratory function in adult patients with spinal muscular atrophy after 1.5 years of treatment

被引:0
|
作者
Simek, Pija Puksic [1 ]
Tratnjek, Manca Groznik [1 ]
Koritnik, Blaz [1 ]
Leonardis, Lea [1 ]
机构
[1] UKC Ljubljana, Ljubljana, Slovenia
关键词
D O I
10.1183/13993003.congress-2024.PA1442
中图分类号
R56 [呼吸系及胸部疾病];
学科分类号
摘要
引用
收藏
页数:2
相关论文
共 50 条
  • [1] The Impact of Nusinersen Treatment on Respiratory Function in Patients with Spinal Muscular Atrophy: A Systematic Review
    Aldukain, Mona
    Aldukain, Ali
    Hobani, Assal
    Barakat, Abdulmalik
    Alsayyed, Lujain
    Alomar, Maher
    Al-Abeden, Maha Saad Zain
    Alzoum, Nora
    Asseri, Ali Alsuheel
    JOURNAL OF CLINICAL MEDICINE, 2024, 13 (21)
  • [2] Impact of Nusinersen treatment on quality of life in adult patients with Spinal Muscular Atrophy
    Castanon, Felix Guerra
    Deardorff, Adam
    Zhao, Songzhu
    Severyn, Steven
    Kelly, Kristrina
    Tellez, Marco
    Heintzman, Sarah
    Sterling, Gary
    Kolb, Stephen
    Arnold, David
    Elsheikh, Bakri
    NEUROLOGY, 2023, 100 (17)
  • [3] Experience of nusinersen treatment to adult patients with spinal muscular atrophy
    Saito, T.
    Matsuoka, Y.
    Odani, H.
    Matsumura, T.
    Nishio, H.
    NEUROMUSCULAR DISORDERS, 2021, 31 : S137 - S138
  • [4] Paediatric spinal muscular atrophy: Longterm nusinersen treatment and respiratory function
    Chacko, A.
    Sly, P.
    Deegan, S.
    Thomas, N.
    Gauld, L.
    RESPIROLOGY, 2022, 27 : 183 - 184
  • [5] NUSINERSEN IN ADULT SPINAL MUSCULAR ATROPHY PATIENTS
    Fadia, Mithila
    Shroff, Sheetal
    Simpson, Ericka
    MUSCLE & NERVE, 2019, 60 : S54 - S54
  • [6] Respiratory function in adult patients with spinal muscular atrophy treated with nusinersen - a monocenter observational study
    Wurster, Claudia Diana
    Uzelac, Zeljko
    Dreyhaupt, Jens
    Schuster, Joachim
    Dorst, Johannes
    Ludolph, Albert Christian
    Wollinsky, Kurt
    FRONTIERS IN NEUROLOGY, 2024, 15
  • [7] Respiratory and Nutritional Effects of Nusinersen Treatment in Spinal Muscular Atrophy Patients
    Zver, A.
    Lepej, D.
    Kotnik, Pirs A.
    Praprotnik, M.
    Setina, Smid S.
    Butenko, T.
    Osredkar, D.
    Krivec, U.
    PEDIATRIC PULMONOLOGY, 2021, 56 : S131 - S131
  • [8] Effect of nusinersen treatment on quality of life and motor function in adult patients with spinal muscular atrophy
    Erdem, Nazan Simsek
    Gencer, Gokce Yagmur Gunes
    Alaamel, Abir
    Uysal, Hilmi
    NEUROMUSCULAR DISORDERS, 2024, 36 : 28 - 32
  • [9] Nusinersen stabilises respiratory function in paediatric spinal muscular atrophy
    Chacko, Archana
    Deegan, Sean
    Gauld, Leanne
    Sly, Peter
    EUROPEAN RESPIRATORY JOURNAL, 2020, 56
  • [10] Feasibility and safety of intrathecal treatment with nusinersen in adult patients with spinal muscular atrophy
    Stolte, Benjamin
    Totzeck, Andreas
    Kizina, Kathrin
    Bolz, Saskia
    Pietruck, Lena
    Moenninghoff, Christoph
    Guberina, Nika
    Oldenburg, Denise
    Forsting, Michael
    Kleinschnitz, Christoph
    Hagenacker, Tim
    THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2018, 11