VASO-OCCLUSION DEFINITIONS CAN IMPACT EFFICACY ASSESSMENTS IN CLINICAL STUDIES OF SICKLE CELL DISEASE

被引：0
|
作者：
Frangoul, H. [1 ]
Imren, S. [2 ]
Xuan, F. [2 ]
Li, N. [2 ]
Rubin, J. L. [2 ]
Hobbs, B. [2 ]
Locatelli, F. [3 ]
机构：
[1] Childrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
[2] Vertex Pharmaceut Inc, Boston, MA USA
[3] Univ Cattolica Sacro Cuore, Osped Pediat Bambino Gesu Rome, IRCCS, Rome, Italy
来源：
VALUE IN HEALTH | 2024年 / 27卷 / 06期
关键词：
D O I：
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中图分类号：
F [经济];
学科分类号：
02 ;
摘要：
CO197
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页码：S54 / S54
页数：1
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