VASO-OCCLUSION DEFINITIONS CAN IMPACT EFFICACY ASSESSMENTS IN CLINICAL STUDIES OF SICKLE CELL DISEASE

被引:0
|
作者
Frangoul, H. [1 ]
Imren, S. [2 ]
Xuan, F. [2 ]
Li, N. [2 ]
Rubin, J. L. [2 ]
Hobbs, B. [2 ]
Locatelli, F. [3 ]
机构
[1] Childrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
[2] Vertex Pharmaceut Inc, Boston, MA USA
[3] Univ Cattolica Sacro Cuore, Osped Pediat Bambino Gesu Rome, IRCCS, Rome, Italy
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F [经济];
学科分类号
02 ;
摘要
CO197
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页码:S54 / S54
页数:1
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