VASO-OCCLUSION DEFINITIONS CAN IMPACT EFFICACY ASSESSMENTS IN CLINICAL STUDIES OF SICKLE CELL DISEASE
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作者:
Frangoul, H.
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Childrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Frangoul, H.
[1
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Imren, S.
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Vertex Pharmaceut Inc, Boston, MA USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Imren, S.
[2
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Xuan, F.
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Vertex Pharmaceut Inc, Boston, MA USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Xuan, F.
[2
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Li, N.
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Vertex Pharmaceut Inc, Boston, MA USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Li, N.
[2
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Rubin, J. L.
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Vertex Pharmaceut Inc, Boston, MA USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Rubin, J. L.
[2
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Hobbs, B.
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Vertex Pharmaceut Inc, Boston, MA USAChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Hobbs, B.
[2
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Locatelli, F.
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Univ Cattolica Sacro Cuore, Osped Pediat Bambino Gesu Rome, IRCCS, Rome, ItalyChildrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
Locatelli, F.
[3
]
机构:
[1] Childrens Hosp TriStar Centennial, Sarah Cannon Res Inst, Nashville, TN USA
机构:
Harvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
Harvard Univ, Sch Med, Brigham & Womens Hosp, Dept Pathol, Boston, MA 02115 USAHarvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
Higgins, J. M.
Eddington, D. T.
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MIT, Div Hlth Sci & Technol, Cambridge, MA 02139 USA
Univ Illinois, Dept Bioengn, Chicago, IL USAHarvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
Eddington, D. T.
Bhatia, S. N.
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MIT, Div Hlth Sci & Technol, Cambridge, MA 02139 USA
MIT, Dept Elect Engn & Comp Sci, Cambridge, MA 02139 USA
Harvard Univ, Sch Med, Brigham & Womens Hosp, Dept Med, Boston, MA 02115 USAHarvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
Bhatia, S. N.
Mahadevan, L.
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Harvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
Harvard Univ, Sch Med, Dept Syst Biol, Boston, MA 02115 USAHarvard Univ, Sch Engn & Appl Sci, Oxford, MA 02138 USA
机构:
Univ Antilles Guyane, INSERM, UMR 665, F-97159 Pointe A Pitre, Guadeloupe, FranceUniv Antilles Guyane, INSERM, UMR 665, F-97159 Pointe A Pitre, Guadeloupe, France
Connes, Philippe
Harmon, Kimberly G.
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机构:
Univ Washington, Dept Family Med, Seattle, WA 98195 USA
Univ Washington, Dept Orthopaed & Sports Med, Seattle, WA 98195 USAUniv Antilles Guyane, INSERM, UMR 665, F-97159 Pointe A Pitre, Guadeloupe, France
Harmon, Kimberly G.
Bergeron, Michael F.
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Sanford USD Med Ctr, Natl Inst Athlet Hlth & Performance, Sioux Falls, SD USAUniv Antilles Guyane, INSERM, UMR 665, F-97159 Pointe A Pitre, Guadeloupe, France