ALTERNATE THERAPIES FOR CYSTIC-FIBROSIS

被引:5
|
作者
MYLETT, J
JOHNSON, K
KNOWLES, M
机构
[1] UNIV N CAROLINA, DIV PULM CRIT CARE & OCCUPAT MED, CHAPEL HILL, NC USA
[2] UNIV N CAROLINA, CTR CYST FIBROSIS PULM RES & TREATMENT, CHAPEL HILL, NC USA
关键词
D O I
10.1055/s-2007-1006387
中图分类号
R4 [临床医学];
学科分类号
1002 ; 100602 ;
摘要
Many new therapeutic approaches show promise for improving the course of pulmonary disease in CF patients. Novel therapies target a spectrum of pathogenic mechanisms, including infection and inflammation, proteolytic enzymes, and abnormal ion transport. Furthermore, gene therapy strives to correct the phenotype in CF by delivering a gene capable of producing functional CFTR. These exciting and promising approaches offer hope that we may soon increase the longevity and quality of life of CF patients.
引用
收藏
页码:426 / 433
页数:8
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