Systematic Literature Review of Clinical and Economic Evidence for Spinal Muscular Atrophy

被引：0
|
作者：
Min Yang
Hiroyuki Awano
Satoru Tanaka
Walter Toro
Su Zhang
Omar Dabbous
Ataru Igarashi
机构：
[1] Analysis Group,Department of Pediatrics
[2] Inc.,Unit of Public Health and Preventive Medicine
[3] Kobe University Graduate School of Medicine,Department of Health Economics and Outcomes Research, Graduate School of Pharmaceutical Sciences
[4] Novartis Pharma K.K.,undefined
[5] Novartis Gene Therapies,undefined
[6] Inc.,undefined
[7] Yokohama City University,undefined
[8] The University of Tokyo,undefined
来源：
Advances in Therapy | 2022年 / 39卷
关键词：
Disease-modifying therapies; Economic burden; Gene therapy; Health-related quality of life; Humanistic burden; Natural history; Nusinersen; Onasemnogene abeparvovec; Spinal muscular atrophy; Systematic literature review;
D O I：
暂无
中图分类号：
学科分类号：
摘要：
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页码：1915 / 1958
页数：43
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