Real-world analysis of healthcare resource utilization by patients with X-linked myotubular myopathy (XLMTM) in the United States

被引：0
|
作者：
Robert J. Graham
Basil T. Darras
Tmirah Haselkorn
Dan Fisher
Casie A. Genetti
Weston Miller
Alan H. Beggs
机构：
[1] Harvard Medical School,Division of Critical Care Medicine, Boston Children’s Hospital
[2] Harvard Medical School,Department of Neurology, Neuromuscular Program, Boston Children’s Hospital
[3] Astellas Gene Therapies,Division of Genetics and Genomics, The Manton Center for Orphan Disease Research, Boston Children’s Hospital
[4] IPM.Ai,undefined
[5] Harvard Medical School,undefined
[6] Formerly of Astellas Gene Therapies,undefined
来源：
Orphanet Journal of Rare Diseases | / 18卷
关键词：
X-linked myotubular myopathy; Congenital myopathy; Insurance claims analysis;
D O I：
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摘要：
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