Development and Evaluation of Cone-Specific Promoters in Non-human Primates for Gene Therapy of Congenital Cone Diseases Including Achromatopsia

被引：0
|
作者：
Ye, Guo-jie [1 ]
Budzynski, Ewa [2 ]
Sonnentag, Peter [2 ]
Nork, Michael [3 ,4 ]
Sheibani, Nader [3 ,4 ]
Boye, Sanford L. [5 ]
Hauswirth, William W. [5 ]
Chulay, Jeffrey D. [1 ]
机构：
[1] AGTC, Alachua, FL USA
[2] Covance Labs Inc, Madison, WI USA
[3] Univ Wisconsin, Madison, WI USA
[4] OSOD LLC, Madison, WI USA
[5] Univ Florida, Gainesville, FL USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2014年 / 55卷 / 13期
关键词：
538 gene transfer/gene therapy; 648; photoreceptors; 688; retina;
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
837
引用
收藏
页数：2
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