Interim Report on the Safety and Efficacy of Longer-term Treatment with Nusinersen in Infantile-onset Spinal Muscular Atrophy (SMA): Updated Results from the SHINE Study

被引：0
|
作者：
Finkel, R.
Castro, D.
Farrar, M.
Tulinius, M.
Krosschell, K.
Saito, K.
Reyna, S.
Zhang, Y.
Bhan, I
Wong, J.
Farwell, W.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Neuromuscular Disorders; Rare Diseases;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
174
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收藏
页码：S122 / S123
页数：2
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