Efficient In Vivo Gene Editing of Inherited Retinal Disease Genes in Mice and Non-Human Primates

被引：0

作者：

Boye, Shannon ^{[1
]}

Stefanidakis, Michael ^{[2
]}

Mepani, Rina ^{[2
]}

Skor, Maxwell N. ^{[2
]}

Gloskowski, Sebastian W. ^{[2
]}

Horng, Joy ^{[2
]}

McCullough, Kevin T. ^{[1
]}

Marco, Eugenio ^{[2
]}

Giannoukos, Georgia ^{[2
]}

Ciulla, Dawn ^{[2
]}

Chao, Hoson ^{[2
]}

Bounoutas, George S. ^{[2
]}

Witherspoon, C. Douglas ^{[3
]}

Wilson, Christopher ^{[2
]}

Bumcrot, David ^{[2
]}

Gamlin, Paul ^{[3
]}

Boye, Sanford ^{[1
]}

Jiang, Haiyan ^{[2
]}

Albright, Charlie ^{[2
]}

Maeder, Morgan L. ^{[2
]}

机构：

[1] Univ Florida, Dept Ophthalmol, Retinal Gene Therapy Grp, Gainesville, FL USA

[2] Editas Med, Cambridge, MA USA

[3] Univ Alabama Birmingham, Dept Ophthalmol, Birmingham, AL 35294 USA

来源：

MOLECULAR THERAPY | 2017年 / 25卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

764

引用

页码：353 / 354

页数：2

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