Genome Editing Using CRISPR/Cas9 and rAAV6 to Functionally Correct Wiskott-Aldrich Syndrome in Human HSPCs

被引：0
|
作者：
Wiebking, Volker [1 ]
Mantri, Sruthi [1 ]
Weinberg, Kenneth I. [1 ]
Porteus, Matthew H. [1 ]
机构：
[1] Stanford Univ, Dept Pediat, Stanford, CA 94305 USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
825
引用
收藏
页码：376 / 377
页数：2
相关论文
共 50 条
  • [31] Efficient Genome Editing in Apple Using a CRISPR/Cas9 system
    Chikako Nishitani
    Narumi Hirai
    Sadao Komori
    Masato Wada
    Kazuma Okada
    Keishi Osakabe
    Toshiya Yamamoto
    Yuriko Osakabe
    Scientific Reports, 6
  • [32] Editing the genome in cells and mice using CRISPR/Cas9 technology
    Herold, M. J.
    Aubrey, B. J.
    Kelly, G. L.
    Kueh, A. J.
    Brennan, M. S.
    O'Connor, L.
    Milla, L.
    Wilcox, S.
    Tai, L.
    Strasser, A.
    EUROPEAN JOURNAL OF IMMUNOLOGY, 2016, 46 : 10 - 10
  • [33] Genome Editing in Plants Using CRISPR/Cas9/sgRNA Technologies
    Weeks, Donald P.
    Jiang, Wenzhi
    IN VITRO CELLULAR & DEVELOPMENTAL BIOLOGY-ANIMAL, 2014, 50 : S21 - S21
  • [34] Comparison of Zinc Finger Nucleases Versus CRISPR-Specific Nucleases for Genome Editing of the Wiskott-Aldrich Syndrome Locus
    Gutierrez-Guerrero, Alejandra
    Sanchez-Hernandez, Sabina
    Galvani, Giuseppe
    Pinedo-Gomez, Javier
    Martin-Guerra, Rocio
    Sanchez-Gilabert, Almudena
    Aguilar-Gonzalez, Araceli
    Cobo, Marien
    Gregory, Philip
    Holmes, Michael
    Benabdellah, Karim
    Martin, Francisco
    HUMAN GENE THERAPY, 2018, 29 (03) : 366 - 380
  • [35] The CRISPR/Cas9 Genome Editing Methodology as a Weapon Against Human Viruses
    White, Martyn K.
    Hu, Wenhui
    Khalili, Kamel
    DISCOVERY MEDICINE, 2015, 19 (105) : 255 - 262
  • [36] CRISPR/Cas9: A revolutionary genome editing tool for human cancers treatment
    Akram, Fatima
    ul Haq, Ikram
    Sahreen, Sania
    Nasir, Narmeen
    Naseem, Waqas
    Imitaz, Memoona
    Aqeel, Amna
    TECHNOLOGY IN CANCER RESEARCH & TREATMENT, 2022, 21
  • [37] The implication of CRISPR/Cas9 genome editing technology in combating human oncoviruses
    Gilani, Usman
    Shaukat, Memoona
    Rasheed, Arisha
    Shahid, Mehak
    Tasneem, Fareeda
    Arshad, Muhammad
    Rashid, Naeem
    Shahzad, Naveed
    JOURNAL OF MEDICAL VIROLOGY, 2019, 91 (01) : 1 - 13
  • [38] Creating cell and animal models of human disease by genome editing using CRISPR/Cas9
    Zarei, Ali
    Razban, Vahid
    Hosseini, Seyed Ebrahim
    Tabei, Seyed Mohammad Bagher
    JOURNAL OF GENE MEDICINE, 2019, 21 (04):
  • [39] CRISPR/Cas9 genome editing to create mouse models for human deafness
    Borodnik-Cohen, Mor
    Danial-Faran, Nada
    Yizhar-Barnea, Ofer
    Noy, Yael
    Koffler, Tal
    Shalev, Stavit
    Haffner, Rebecca
    Avraham, Karen B.
    HUMAN GENOMICS, 2018, 12
  • [40] Beta-Globin Gene Targeting in Human Hematopoietic Stem Cells Using Cas9 Ribonucleoprotein and rAAV6
    Dever, Daniel Patrick
    Porteus, Matthew
    BLOOD, 2016, 128 (22)
12345