An engineered self-inactivating adeno-associated virus mediated Cas9 delivery system for therapeutic genome editing

被引:0
|
作者
Fuentes, C. M. [1 ]
Chen, A. [1 ]
Schaffer, D. V. [1 ]
机构
[1] Univ Calif Berkeley, Berkeley, CA 94720 USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
P564
引用
收藏
页码:A183 / A183
页数:1
相关论文
共 50 条
  • [21] Genome editing via delivery of Cas9 ribonucleoprotein
    DeWitt, Mark A.
    Corn, Jacob E.
    Carroll, Dana
    METHODS, 2017, 121 : 9 - 15
  • [22] Advances in therapeutic CRISPR/Cas9 genome editing
    Schwank, G.
    EUROPEAN JOURNAL OF HUMAN GENETICS, 2019, 27 : 1053 - 1053
  • [23] Efficient virus-mediated genome editing in cotton using the CRISPR/Cas9 system
    Lei, Jianfeng
    Li, Yue
    Dai, Peihong
    Liu, Chao
    Zhao, Yi
    You, Yangzi
    Qu, Yanying
    Chen, Quanjia
    Liu, Xiaodong
    FRONTIERS IN PLANT SCIENCE, 2022, 13
  • [24] Efficient Virus-Mediated Genome Editing in Plants Using the CRISPR/Cas9 System
    Ali, Zahir
    Abul-faraj, Aala
    Li, Lixin
    Ghosh, Neha
    Piatek, Marek
    Mahjoub, Ali
    Aouida, Mustapha
    Piatek, Agnieszka
    Baltes, Nicholas J.
    Voytas, Daniel F.
    Dinesh-Kumar, Savithramma
    Mahfouz, Magdy M.
    MOLECULAR PLANT, 2015, 8 (08) : 1288 - 1291
  • [25] Advances in therapeutic CRISPR/Cas9 genome editing
    Savic, Natasa
    Schwank, Gerald
    TRANSLATIONAL RESEARCH, 2016, 168 : 15 - 21
  • [26] Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
    Ibraheim, Raed
    Tai, Phillip W. L.
    Mir, Aamir
    Javeed, Nida
    Wang, Jiaming
    Rodriguez, Tomas C.
    Namkung, Suk
    Nelson, Samantha
    Khokhar, Eraj Shafiq
    Mintzer, Esther
    Maitland, Stacy
    Chen, Zexiang
    Cao, Yueying
    Tsagkaraki, Emmanouela
    Wolfe, Scot A.
    Wang, Dan
    Pai, Athma A.
    Xue, Wen
    Gao, Guangping
    Sontheimer, Erik J.
    NATURE COMMUNICATIONS, 2021, 12 (01)
  • [27] Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
    Raed Ibraheim
    Phillip W. L. Tai
    Aamir Mir
    Nida Javeed
    Jiaming Wang
    Tomás C. Rodríguez
    Suk Namkung
    Samantha Nelson
    Eraj Shafiq Khokhar
    Esther Mintzer
    Stacy Maitland
    Zexiang Chen
    Yueying Cao
    Emmanouela Tsagkaraki
    Scot A. Wolfe
    Dan Wang
    Athma A. Pai
    Wen Xue
    Guangping Gao
    Erik J. Sontheimer
    Nature Communications, 12
  • [28] Long-Term Effects of In Vivo Genome Editing in the Mouse Retina Using Campylobacter jejuni Cas9 Expressed via Adeno-Associated Virus
    Jo, Dong Hyun
    Koo, Taeyoung
    Cho, Chang Sik
    Kim, Jin Hyoung
    Kim, Jin-Soo
    Kim, Jeong Hun
    MOLECULAR THERAPY, 2019, 27 (01) : 130 - 136
  • [29] Long-term effects of in vivo genome editing in the mouse retina using Campylobacter jejuni Cas9 expressed via adeno-associated virus
    Kim, J.
    Jo, D.
    Kim, J.
    BRITISH JOURNAL OF PHARMACOLOGY, 2019, 176 (16) : 2984 - 2984
  • [30] Nanoparticle-mediated delivery of the CRISPR/Cas9 system components into plant cell for genome editing
    Makhotenko, A.
    Makarov, V.
    Snigir, E.
    Khromov, A.
    Makarova, S.
    Kalinina, N.
    Taliansky, M.
    FEBS JOURNAL, 2017, 284 : 168 - 168