Long-Term Correction of Glycogen Storage Disease Type III by AAV-Mediated Gene Therapy Using a Dual Promoter to Express Bacterial Pullulanase

被引：0
|
作者：
Lim, Jeong-A [1 ]
Choi, Su Jin [1 ]
Kishnani, Priya S. [1 ]
Sun, Baodong [1 ]
机构：
[1] Duke Univ, Durham, NC USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
246
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页码：119 / 120
页数：2
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