Bicistronic AAV Gene Therapy for Tay-Sachs and Sandhoff Diseases

被引：0

作者：

Taghian, Toloo ^{[1
]}

Fernau, Deborah ^{[1
]}

Mercado, Kalajan L. ^{[2
]}

Ellis, Lauren ^{[2
]}

Diffie, Elise ^{[2
]}

Gross, Amanda ^{[2
]}

Maguire, Anne S. ^{[2
]}

Batista, Ana Rita ^{[1
]}

Bertrand, Stephanie ^{[3
]}

Otero, Monique ^{[1
]}

Prestigiacomo, Rachel ^{[3
]}

Gately, Rachael ^{[3
]}

Gallagher, Jillian ^{[1
]}

Lahey, Hannah ^{[1
]}

Taylor, Amanda ^{[2
]}

Koehler, Jey ^{[2
]}

Martin, Douglas R. ^{[2
]}

Sena-Esteves, Miguel ^{[1
]}

Gray-Edwards, Heather L. ^{[1
]}

机构：

[1] Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA

[2] Auburn Univ, Auburn, AL 36849 USA

[3] Tufts Cummings Sch Vet Med, Grafton, MA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

135

引用

页码：68 / 68

页数：1

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