Bicistronic AAV Gene Therapy for Tay-Sachs and Sandhoff Diseases

被引：0
|
作者：
Taghian, Toloo [1 ]
Fernau, Deborah [1 ]
Mercado, Kalajan L. [2 ]
Ellis, Lauren [2 ]
Diffie, Elise [2 ]
Gross, Amanda [2 ]
Maguire, Anne S. [2 ]
Batista, Ana Rita [1 ]
Bertrand, Stephanie [3 ]
Otero, Monique [1 ]
Prestigiacomo, Rachel [3 ]
Gately, Rachael [3 ]
Gallagher, Jillian [1 ]
Lahey, Hannah [1 ]
Taylor, Amanda [2 ]
Koehler, Jey [2 ]
Martin, Douglas R. [2 ]
Sena-Esteves, Miguel [1 ]
Gray-Edwards, Heather L. [1 ]
机构：
[1] Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
[2] Auburn Univ, Auburn, AL 36849 USA
[3] Tufts Cummings Sch Vet Med, Grafton, MA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
135
引用
收藏
页码：68 / 68
页数：1
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