Preclinical development of an efficient and safe gene editing platform for the treatment of Wiskott Aldrich Syndrome

被引：0
|
作者：
Naseem, A. [1 ]
Turchiano, G. [1 ]
Rai, R. [1 ]
Vetharoy, W. [1 ]
Whittaker, T. E. [1 ]
Thrasher, A. J. [1 ,2 ]
Cavazza, A.
机构：
[1] UCL Inst Child Hlth, London, England
[2] NIHR Great Ormond St Hosp, Biomed Res Ctr, London, England
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P667
引用
收藏
页码：A202 / A203
页数：2
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