Correcting SMN2 splicing with tailed antisense oligoribonucleotides: a promising therapeutic strategy for spinal muscular atrophy

被引：0

作者：

Zhou, H. ^{[1
]}

Owen, N. ^{[2
]}

Eperon, I. C. ^{[2
]}

Muntoni, F. ^{[1
]}

机构：

[1] UCL, Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England

[2] Univ Leicester, Dept Biochem, Leicester LE1 7RH, Leics, England

来源：

NEUROMUSCULAR DISORDERS | 2009年 / 19卷 / 8-9期

关键词：

D O I：

10.1016/j.nmd.2009.06.112

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：578 / 578

页数：1

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